Silencing of mutant ATXN3 through antisense oligonucleotides rescues molecular and neuropathological features in Machado-Joseph disease mice

被引：0
|
作者：
Silva, A. C. [1 ,2 ,3 ,4 ]
Lobo, D. D. [1 ,2 ,3 ,4 ]
Henriques, C. [1 ,2 ,4 ,5 ]
Martins, I. M. [1 ,2 ,3 ]
Lopes, S. M. [1 ,2 ,3 ]
Duarte, S. P. [1 ,2 ,3 ]
Wagner, E. [6 ]
Nobre, R. J. [1 ,2 ,3 ,4 ]
Pereira de Almeida, L. [1 ,2 ,3 ,4 ,5 ]
机构：
[1] Univ Coimbra, CNC Ctr Neurosci & Cell Biol, Coimbra, Portugal
[2] Univ Coimbra, CIBB Ctr Innovat Biomed & Biotechnol, Coimbra, Portugal
[3] Univ Coimbra, Inst Interdisciplinary Res, Coimbra, Portugal
[4] Univ Coimbra, Viral Vector Gene Transfer Core Facil, ViraVector, Coimbra, Portugal
[5] Univ Coimbra, Fac Pharm, Coimbra, Portugal
[6] Wave Life Sci Ltd, Cambridge, MA USA
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P214
引用
收藏
页码：A83 / A83
页数：1
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