Intrathecal Lumbar Administration of AAV9 in Nonhuman Primates is Safe and Effective in Targeting Cells of the Central Nervous System

被引：0
|
作者：
Foust, Kevin [1 ]
Thomsen, Gretchen M. [1 ]
Fugere, Martin [1 ]
Chu, Binh [1 ]
Do, Janet [1 ]
Hsieh, Caroline [1 ]
Solano, Stephanie [1 ]
Morales, Pablo [2 ]
Kaspar, Allan [1 ]
Kaspar, Brian K. [1 ]
机构：
[1] AveXis Res & Dev, San Diego, CA USA
[2] Mannheimer Fdn Inc, Homestead, FL USA
来源：
MOLECULAR THERAPY | 2019年 / 27卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
186
引用
收藏
页码：97 / 97
页数：1
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