Amyotrophic Lateral Sclerosis gene therapy using recombinant AAV9 vectors to silence the mutant SOD1 gene

被引：0
|
作者：
Biferi, M. G. [1 ]
Roda, M. [1 ]
Barkats, M. [1 ]
机构：
[1] Inst Myol, UPMC CNRS AIM INSERM UMRS 974, Grp SNC Motoneurone, Equipe Biotherapie Malad Neuromusculaires, F-75013 Paris, France
来源：
HUMAN GENE THERAPY | 2012年 / 23卷 / 05期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
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页码：A17 / A17
页数：1
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