Stable Factor IX Activity Following AAV-mediated Gene Transfer in Patients with Severe Hemophilia B.

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作者
Nathwani, Amit [1 ,2 ]
机构
[1] UCL, London, England
[2] Royal Free Hosp, London NW3 2QG, England
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Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
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页码:A16 / A16
页数:1
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