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- [1] CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis NEW ENGLAND JOURNAL OF MEDICINE, 2021, 385 (18): : 1722 - 1722
- [2] CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis NEW ENGLAND JOURNAL OF MEDICINE, 2021, 385 (06): : 493 - 502
- [3] Controlling CRISPR-Cas9 Gene Editing NEW ENGLAND JOURNAL OF MEDICINE, 2019, 381 (03): : 289 - 290