[1] Childrens Hosp, Boston, MA 02115 USA
[2] Case Western Reserve Univ, Sch Med, Cleveland, OH USA
[3] Emory Univ, Sch Med, Atlanta, GA USA
[4] ICON Late Phase & Outcomes Res, San Francisco, CA USA
[5] Genentech Inc, San Francisco, CA 94080 USA
[6] Univ Arizona, Tucson, AZ USA