Preclinical development of an ex vivo gene therapy for Mucopolysaccharidosis type II

被引：0
|
作者：
Das, S. [1 ]
Rruga, F. [2 ]
Rigon, L. [2 ]
Patel, J. [1 ]
Milazzo, R. [2 ]
Poletti, V. [1 ,2 ]
Biffi, A. [2 ]
机构：
[1] Harvard Med Sch, Boston Childrens Canc & Blood Disorders Ctr, Dana Farber, Boston, MA USA
[2] Univ Padua, Womans & Child Hlth, Dept Pediat, Hematol & Oncol Ctr, Padua, Italy
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR04
引用
收藏
页码：A3 / A3
页数：1
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