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- [1] A humanized mouse model for adeno-associated viral gene therapyNATURE COMMUNICATIONS, 2024, 15 (01)Barzi, Mercedes论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAChen, Tong论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USA Duke Univ, Med Ctr, Dept Mol Genet & Microbiol, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAGonzalez, Trevor J.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Dept Mol Genet & Microbiol, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAPankowicz, Francis P.论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Ctr Cell & Gene Therapy, Stem Cells & Regenerat Med Ctr, Houston, TX 77030 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAOh, Seh Hoon论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Dept Med, Div Gastroenterol, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAStreff, Helen L.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Pratt Sch Engn, Dept Biomed Engn, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USARosales, Alan论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Pratt Sch Engn, Dept Biomed Engn, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAMa, Yunhan论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USACollias, Sabrina论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAWoodfield, Sarah E.论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Michael E DeBakey Dept Surg, Div Pediat Surg, Houston, TX 77030 USA Baylor Coll Med, Michael E DeBakey Dept Surg, Div Surg Res, Houston, TX 77030 USA Texas Childrens Hosp, Dept Surg, Houston, TX 77030 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USADiehl, Anna Mae论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Dept Med, Div Gastroenterol, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAVasudevan, Sanjeev A.论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Michael E DeBakey Dept Surg, Div Pediat Surg, Houston, TX 77030 USA Baylor Coll Med, Michael E DeBakey Dept Surg, Div Surg Res, Houston, TX 77030 USA Texas Childrens Hosp, Dept Surg, Houston, TX 77030 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAGalvan, Thao N.论文数: 0 引用数: 0 h-index: 0机构: Texas Childrens Hosp, Dept Surg, Houston, TX 77030 USA Baylor Coll Med, Michael E DeBakey Dept Surg, Div Hepatobiliary Surg, Houston, TX 77030 USA Baylor Coll Med, Div Hepatobiliary Surg, Houston, TX 77030 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAGoss, John论文数: 0 引用数: 0 h-index: 0机构: Texas Childrens Hosp, Dept Surg, Houston, TX 77030 USA Baylor Coll Med, Michael E DeBakey Dept Surg, Div Hepatobiliary Surg, Houston, TX 77030 USA Baylor Coll Med, Div Hepatobiliary Surg, Houston, TX 77030 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USAGersbach, Charles A.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Pratt Sch Engn, Dept Biomed Engn, Durham, NC 27710 USA Duke Univ, Duke Canc Ctr, Med Ctr, Durham, NC 27710 USA Duke Univ, Med Ctr, Dept Surg, Durham, NC 27710 USA Duke Univ, Duke Regenerat Ctr, Sch Med, Durham, NC 27710 USA Duke Univ, Ctr Adv Genom Technol, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USA论文数: 引用数: h-index:机构:Asokan, Aravind论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Med Ctr, Dept Mol Genet & Microbiol, Durham, NC 27710 USA Duke Univ, Pratt Sch Engn, Dept Biomed Engn, Durham, NC 27710 USA Duke Univ, Med Ctr, Dept Surg, Durham, NC 27710 USA Duke Univ, Duke Regenerat Ctr, Sch Med, Durham, NC 27710 USA Duke Univ, Ctr Adv Genom Technol, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USABissig, Karl-Dimiter论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USA Duke Univ, Med Ctr, Dept Med, Div Gastroenterol, Durham, NC 27710 USA Duke Univ, Pratt Sch Engn, Dept Biomed Engn, Durham, NC 27710 USA Duke Univ, Duke Canc Ctr, Med Ctr, Durham, NC 27710 USA Duke Univ, Duke Regenerat Ctr, Sch Med, Durham, NC 27710 USA Duke Univ, Ctr Adv Genom Technol, Durham, NC 27710 USA Duke Univ, Dept Pharmacol & Canc Biol, Med Ctr, Durham, NC 27710 USA Duke Univ, Alice & YT Chen Ctr Genet & Genom, Dept Pediat, Div Med Genet,Med Ctr, Durham, NC 27710 USA
- [2] A humanized mouse model for adeno-associated viral gene therapyNature Communications, 15Mercedes Barzi论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsTong Chen论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsTrevor J. Gonzalez论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsFrancis P. Pankowicz论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsSeh Hoon Oh论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsHelen L. Streff论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsAlan Rosales论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsYunhan Ma论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsSabrina Collias论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsSarah E. Woodfield论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsAnna Mae Diehl论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsSanjeev A. Vasudevan论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsThao N. Galvan论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsJohn Goss论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsCharles A. Gersbach论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsBeatrice Bissig-Choisat论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsAravind Asokan论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of PediatricsKarl-Dimiter Bissig论文数: 0 引用数: 0 h-index: 0机构: Duke University Medical Center,Alice and Y. T. Chen Center for Genetics and Genomics, Division of Medical Genetics, Department of Pediatrics
- [3] Efficient gene transfer to the pancreas using adeno-associated viral vectors for prevention of type 1 diabetes in miceDIABETOLOGIA, 2010, 53 : S176 - S176Casellas, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainJimenez, V.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainAyuso, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainAgudo, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainObach, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainSalavert, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainMunoz, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainMoya, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainLeon, X.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainMolas, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainRamos, D.论文数: 0 引用数: 0 h-index: 0机构: CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Anim Hlth & Anat, Bellaterra, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainRuberte, J.论文数: 0 引用数: 0 h-index: 0机构: CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Anim Hlth & Anat, Bellaterra, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, SpainBosch, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain Univ Autonoma Barcelona, CBATEG, Bellaterra, Spain CIBER Diabet & Associated Metab Disorders, Barcelona, Spain Univ Autonoma Barcelona, Sch Vet Med, Dept Biochem & Mol Biol, Bellaterra, Spain
- [4] Adeno-Associated Viral Vectors for Gene TherapyOPHTHALMOLOGICA, 2014, 232 : 8 - 9Dalkara, Deniz论文数: 0 引用数: 0 h-index: 0机构: INSERM, UMR S 968, Inst Vis, F-75012 Paris, France Sorbonne Univ, Univ Paris 06, UMR S 968, Inst Vis, F-75012 Paris, France CNRS, UMR 7210, F-75012 Paris, France INSERM, UMR S 968, Inst Vis, F-75012 Paris, France
- [5] Adeno-associated viral vectors for gene therapyBIOGENIC AMINES, 1998, 14 (05) : 451 - 475Summerford, C论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USASamulski, RJ论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27599 USA
- [6] Adeno-associated viral gene therapy corrects a mouse model of argininosuccinic aciduriaMOLECULAR GENETICS AND METABOLISM, 2018, 125 (03) : 241 - 250Ashley, Scott N.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USANordin, Jayme M. L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USABuza, Elizabeth L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAGreig, Jenny A.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USAWilson, James M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA
- [7] Interleukin-10 gene therapy utilizing adeno-associated virus vectors prevents type 1 diabetes in NOD miceDIABETES, 2001, 50 : A33 - A33Goudy, K论文数: 0 引用数: 0 h-index: 0Ellis, T论文数: 0 引用数: 0 h-index: 0Ottendorfer, E论文数: 0 引用数: 0 h-index: 0Song, SH论文数: 0 引用数: 0 h-index: 0Wasserfall, C论文数: 0 引用数: 0 h-index: 0Flotte, T论文数: 0 引用数: 0 h-index: 0Atkinson, M论文数: 0 引用数: 0 h-index: 0
- [8] Hepatotoxicity in Adeno-Associated Viral Vector Gene TherapyCurrent Hepatology Reports, 2023, 22 (4) : 276 - 290Jagadisan B.论文数: 0 引用数: 0 h-index: 0机构: Pediatric Liver GI and Nutrition Centre and Mowat Labs, King’s College Hospital NHS Foundation Trust, Denmark Hill, London Pediatric Liver GI and Nutrition Centre and Mowat Labs, King’s College Hospital NHS Foundation Trust, Denmark Hill, LondonDhawan A.论文数: 0 引用数: 0 h-index: 0机构: Pediatric Liver GI and Nutrition Centre and Mowat Labs, King’s College Hospital NHS Foundation Trust, Denmark Hill, London Pediatric Liver GI and Nutrition Centre and Mowat Labs, King’s College Hospital NHS Foundation Trust, Denmark Hill, London
- [9] A role for adeno-associated viral vectors in gene therapyGENETICS AND MOLECULAR BIOLOGY, 2008, 31 (01) : 1 - 11Coura, Renata dos Santos论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio Grande do Sul, Dept Genet, Lab Imunogenet, BR-91501970 Porto Alegre, RS, Brazil Univ Fed Rio Grande do Sul, Dept Genet, Lab Imunogenet, BR-91501970 Porto Alegre, RS, BrazilNardi, Nance Beyer论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio Grande do Sul, Dept Genet, Lab Imunogenet, BR-91501970 Porto Alegre, RS, Brazil Univ Fed Rio Grande do Sul, Dept Genet, Lab Imunogenet, BR-91501970 Porto Alegre, RS, Brazil
- [10] Tailoring adeno-associated viral vectors for gene transfer and gene therapyHUMAN GENE THERAPY, 2011, 22 (06) : A3 - A3Buening, Hildegard论文数: 0 引用数: 0 h-index: 0机构: Univ Cologne, Dept Internal Med 1, Cologne, Germany Univ Cologne, Ctr Mol Med Cologne ZMMK, Cologne, Germany Univ Cologne, Dept Internal Med 1, Cologne, Germany