Expression of human FIX at therapeutic levels in nonhuman primates following a single peripheral vein infusion of low doses of self complementary AAV vector renews hope for haemophilia B gene therapy

被引：0
|
作者：
Mcintosh, J
Cochrane, M
Tuddenham, EGD
Davidoff, AM
Nathwani, AC
机构：
[1] UCL, Dept Haematol, London, England
[2] Royal Free Hosp, Katharine Dormandy Haemophilia Ctr, London NW3 2QG, England
[3] Royal Free Hosp, Haemostasis Unit, London NW3 2QG, England
[4] St Jude Childrens Hosp, Dept Surg, Memphis, TN 38105 USA
来源：
BRITISH JOURNAL OF HAEMATOLOGY | 2006年 / 133卷
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中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
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页码：18 / 18
页数：1
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