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- [1] Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy A Randomized Clinical TrialJAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2022, 327 (15): : 1456 - 1468Guglieri, Michela论文数: 0 引用数: 0 h-index: 0机构: Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England Newcastle Hosp NHS Fdn Trust, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandBushby, Kate论文数: 0 引用数: 0 h-index: 0机构: Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England Newcastle Hosp NHS Fdn Trust, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandMcDermott, Michael P.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Med Ctr, Rochester, NY USA Univ Rochester, Dept Biostat & Computat Biol, Med Ctr, Rochester, NY USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandHart, Kimberly A.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Med Ctr, Rochester, NY USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandTawil, Rabi论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Med Ctr, Rochester, NY USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandMartens, William B.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Med Ctr, Rochester, NY USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandHerr, Barbara E.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Med Ctr, Rochester, NY USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England论文数: 引用数: h-index:机构:Speed, Chris论文数: 0 引用数: 0 h-index: 0机构: Newcastle Univ, Newcastle Upon Tyne, Tyne & Wear, England NIHR Clin Res Network North East & North Cumbria, Newcastle Upon Tyne, Tyne & Wear, England Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England论文数: 引用数: h-index:机构:Kirschner, Janbernd论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Freiburg, Dept Neuropediat & Muscle Disorders, Fac Med, Freiburg, Germany Univ Hosp Bonn, Dept Neuropediat, Bonn, Germany Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandKing, Wendy M.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Columbus, OH 43210 USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandEagle, Michelle论文数: 0 引用数: 0 h-index: 0机构: Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England Newcastle Hosp NHS Fdn Trust, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandBrown, Mary W.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Med Ctr, Rochester, NY USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandWillis, Tracey论文数: 0 引用数: 0 h-index: 0机构: NHS Fdn Trust, Robert Jones & Agnes Hunt Orthopaed Hosp, Oswestry, Shrops, England Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, EnglandGriggs, Robert C.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Dept Neurol, Med Ctr, Rochester, NY USA Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne NE13 BZ, Tyne & Wear, England
- [2] Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy A Randomized Clinical TrialJAMA NEUROLOGY, 2022, 79 (10) : 1005 - 1014论文数: 引用数: h-index:机构:Clemens, Paula R.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Sch Med, Pittsburgh, PA USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandPerlman, Seth J.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, Seattle, WA USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandSmith, Edward C.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Durham, NC USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandHorrocks, Iain论文数: 0 引用数: 0 h-index: 0机构: Royal Hosp Children, Glasgow, Lanark, Scotland Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandFinkel, Richard S.论文数: 0 引用数: 0 h-index: 0机构: Nemours Childrens Hosp, Orlando, FL USA St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandMah, Jean K.论文数: 0 引用数: 0 h-index: 0机构: Univ Calgary, Alberta Childrens Hosp, Res Inst, Calgary, AB, Canada Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandDeconinck, Nicolas论文数: 0 引用数: 0 h-index: 0机构: UZ Ghent, Neuromuscular Reference Ctr, Ghent, Belgium Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandGoemans, Nathalie论文数: 0 引用数: 0 h-index: 0机构: Katholieke Univ Leuven, Dept Dev & Regenerat, Leuven, Belgium Univ Hosp Leuven, Dept Paediat Neurol, Leuven, Belgium Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandHaberlova, Jana论文数: 0 引用数: 0 h-index: 0机构: Charles Univ Prague, Motol Univ Hosp, Neuromuscular Ctr, Med Sch 2,Dept Pediat Neurol, Prague, Czech Republic Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandStraub, Volker论文数: 0 引用数: 0 h-index: 0机构: Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England Newcastle Univ, Newcastle Upon Tyne, Tyne & Wear, England Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandMengle-Gaw, Laurel J.论文数: 0 引用数: 0 h-index: 0机构: Camden Grp, St Louis, MO USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandSchwartz, Benjamin D.论文数: 0 引用数: 0 h-index: 0机构: Camden Grp, St Louis, MO USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandHarper, Amy D.论文数: 0 引用数: 0 h-index: 0机构: Richmond Childrens Hosp, Richmond, VA USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandShieh, Perry B.论文数: 0 引用数: 0 h-index: 0机构: UCLA Med Sch, Los Angeles, CA USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandDe Waele, Liesbeth论文数: 0 引用数: 0 h-index: 0机构: Katholieke Univ Leuven, Dept Dev & Regenerat, Leuven, Belgium Univ Hosp Leuven, Dept Paediat Neurol, Leuven, Belgium Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandCastro, Diana论文数: 0 引用数: 0 h-index: 0机构: UT Southwestern Med Ctr, Dallas, TX USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandYang, Michelle L.论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Childrens Hosp Colorado, Sch Med, Aurora, CO USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandRyan, Monique M.论文数: 0 引用数: 0 h-index: 0机构: Royal Childrens Hosp, Melbourne, Vic, Australia Murdoch Childrens Res Inst, Melbourne, Vic, Australia Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandMcDonald, Craig M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA 95817 USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandTulinius, Mar论文数: 0 引用数: 0 h-index: 0机构: Queen Silvia Childrens Hosp, Gothenburg, Sweden Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandWebster, Richard论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Westmead, Kids Neurosci Ctr, Westmead, NSW, Australia Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandMcMillan, Hugh J.论文数: 0 引用数: 0 h-index: 0机构: Univ Ottawa, Ottawa, ON, Canada Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandKuntz, Nancy L.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp, Chicago, IL USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandRao, Vashmi K.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp, Chicago, IL USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandBaranello, Giovanni论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Great Ormond St Hosp,Biomed Res Ctr, Natl Inst Hlth Res,Dubowitz Neuromuscular Ctr, London, England Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandSpinty, Stefan论文数: 0 引用数: 0 h-index: 0机构: Alder Hey Childrens NHS Fdn Trust, Liverpool, Merseyside, England Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandChilds, Anne-Marie论文数: 0 引用数: 0 h-index: 0机构: Leeds Teaching Hosp Trust, Leeds, W Yorkshire, England Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandSbrocchi, Annie M.论文数: 0 引用数: 0 h-index: 0机构: Montreal Childrens Hosp, Montreal, PQ, Canada Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandSelby, Kathryn A.论文数: 0 引用数: 0 h-index: 0机构: BC Childrens Hosp Res Inst, Vancouver, BC, Canada Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandMonduy, Migvis论文数: 0 引用数: 0 h-index: 0机构: Nemours Childrens Hosp, Orlando, FL USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandNevo, Yoram论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Schneider Childrens Med Ctr, Tel Aviv, Israel Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandVilchez-Padilla, Juan J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Quironsalud Valencia, Valencia, Spain Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandNascimento-Osorio, Andres论文数: 0 引用数: 0 h-index: 0机构: Inst Recerca Pediat Hosp St Joan de Deu, Neuropaediat Dept, Barcelona, Spain Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandNiks, Erik H.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Leiden, Netherlands Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, Englandde Groot, Imelda J. M.论文数: 0 引用数: 0 h-index: 0机构: Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlands Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandKatsalouli, Marina论文数: 0 引用数: 0 h-index: 0机构: PA Kyriakou Childrens Hosp, Athens, Greece Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandJames, Meredith K.论文数: 0 引用数: 0 h-index: 0机构: Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England Newcastle Univ, Newcastle Upon Tyne, Tyne & Wear, England Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, Englandvan den Anker, Johannes论文数: 0 引用数: 0 h-index: 0机构: ReveraGen BioPharma, Rockville, MD USA Childrens Natl Med Ctr, Washington, DC 20010 USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandDamsker, Jesse M.论文数: 0 引用数: 0 h-index: 0机构: ReveraGen BioPharma, Rockville, MD USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandAhmet, Alexandra论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Eastern Ontario, Res Inst, Ottawa, ON, Canada Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandWard, Leanne M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Eastern Ontario, Res Inst, Ottawa, ON, Canada Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandJaros, Mark论文数: 0 引用数: 0 h-index: 0机构: Summit Analyt, Denver, CO USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandShale, Phil论文数: 0 引用数: 0 h-index: 0机构: Summit Analyt, Denver, CO USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandDang, Utkarsh J.论文数: 0 引用数: 0 h-index: 0机构: Carleton Univ, Ottawa, ON, Canada Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, EnglandHoffman, Eric P.论文数: 0 引用数: 0 h-index: 0机构: ReveraGen BioPharma, Rockville, MD USA SUNY Binghamton, Sch Pharm & Pharmaceut Sci, Dept Pharmaceut Sci, POB 6000, Binghamton, NY 13902 USA Newcastle Hosp NHS Fdn Trust, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England
- [3] Myoglobinuria in boys with Duchenne muscular dystrophy on corticosteroid therapyNEUROMUSCULAR DISORDERS, 2008, 18 (01) : 71 - 73Garrood, P.论文数: 0 引用数: 0 h-index: 0机构: Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandEagle, M.论文数: 0 引用数: 0 h-index: 0机构: Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandJardine, P. E.论文数: 0 引用数: 0 h-index: 0机构: Bristol Childrens Hosp, Bristol BS2 8BJ, Avon, England Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandBushby, K.论文数: 0 引用数: 0 h-index: 0机构: Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, EnglandStraub, V.论文数: 0 引用数: 0 h-index: 0机构: Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England Int Ctr Life, Inst Human Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England
- [4] Randomized, Double-blind Controlled Trial Assessing The Dose Response And Safety Of Deflazacort In Boys With Duchenne Muscular DystrophyNEUROLOGY, 2021, 96 (15)Reddy, Chaithanya论文数: 0 引用数: 0 h-index: 0机构: PGIMER, Pediat, Chandigarh, India PGIMER, Pediat, Chandigarh, IndiaSuthar, Renu论文数: 0 引用数: 0 h-index: 0机构: PGIMER, Pediat, Chandigarh, India PGIMER, Pediat, Chandigarh, IndiaPatil, Amol论文数: 0 引用数: 0 h-index: 0机构: PGIMER, Pharmacol, Chandigarh, India PGIMER, Pediat, Chandigarh, IndiaSaxena, Somya论文数: 0 引用数: 0 h-index: 0机构: PGIMER, Phys Med & Rehabil, Chandigarh, India PGIMER, Pediat, Chandigarh, IndiaSaini, Arushi G.论文数: 0 引用数: 0 h-index: 0机构: PGIMER, Pediat, Chandigarh, India PGIMER, Pediat, Chandigarh, IndiaSankhyan, Naveen论文数: 0 引用数: 0 h-index: 0机构: PGIMER, Pediat, Chandigarh, India PGIMER, Chandigarh, India PGIMER, Pediat, Chandigarh, IndiaSankhyan, Naveen论文数: 0 引用数: 0 h-index: 0机构: PGIMER, Pediat, Chandigarh, India PGIMER, Chandigarh, India PGIMER, Pediat, Chandigarh, India
- [5] Assisted bicycle training delays physical deterioration in boys with Duchenne muscular dystrophy: Results of the randomized controlled trial "no use is disuse"NEUROMUSCULAR DISORDERS, 2011, 21 (9-10) : 658 - 658Jansen, M.论文数: 0 引用数: 0 h-index: 0机构: Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlands Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlandsvan Alfen, N.论文数: 0 引用数: 0 h-index: 0机构: Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlands Radboud Univ Nijmegen Med Ctr, Nijmegen, NetherlandsGeurts, A. C. H.论文数: 0 引用数: 0 h-index: 0机构: Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlands Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlandsde Groot, I. J. M.论文数: 0 引用数: 0 h-index: 0机构: Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlands Radboud Univ Nijmegen Med Ctr, Nijmegen, Netherlands
- [6] Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular DystrophyNEUROLOGY, 2024, 102 (05)Dang, Utkarsh J.论文数: 0 引用数: 0 h-index: 0机构: Carleton Univ, Ottawa, ON, Canada Carleton Univ, Ottawa, ON, CanadaDamsker, Jesse M.论文数: 0 引用数: 0 h-index: 0机构: ReveraGen Biopharm, Rockville, MD 20850 USA Carleton Univ, Ottawa, ON, Canada论文数: 引用数: h-index:机构:Clemens, Paula R.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Sch Med, Pittsburgh, PA USA Univ Pittsburgh, Dept Vet Affairs Med Ctr, Pittsburgh, PA USA Carleton Univ, Ottawa, ON, CanadaPerlman, Seth J.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, Seattle, WA USA Carleton Univ, Ottawa, ON, CanadaSmith, Edward C.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Durham, NC USA Carleton Univ, Ottawa, ON, CanadaHorrocks, Iain论文数: 0 引用数: 0 h-index: 0机构: Royal Hosp Children, Glasgow, Scotland Carleton Univ, Ottawa, ON, CanadaFinkel, Richard S.论文数: 0 引用数: 0 h-index: 0机构: Nemours Childrens Hosp, Orlando, FL USA St Jude Childrens Res Hosp, Memphis, TN USA Carleton Univ, Ottawa, ON, CanadaMah, Jean K.论文数: 0 引用数: 0 h-index: 0机构: Univ Calgary, Alberta Childrens Hosp Res Inst, Calgary, AB, Canada Carleton Univ, Ottawa, ON, CanadaDeconinck, Nicolas论文数: 0 引用数: 0 h-index: 0机构: UZ Ghent, Neuromuscular Reference Ctr NMRC, Ghent, Belgium Carleton Univ, Ottawa, ON, CanadaGoemans, Nathalie M.论文数: 0 引用数: 0 h-index: 0机构: Katholieke Univ Leuven, Dept Dev & Regenerat, Leuven, Belgium Univ Hosp Leuven, Dept Paediat Neurol, Leuven, Belgium Carleton Univ, Ottawa, ON, CanadaHaberlova, Jana论文数: 0 引用数: 0 h-index: 0机构: Motol Univ Hosp, Neuromuscular Ctr, Dept Pediat Neurol, Prague, Czech Republic Charles Univ Prague, Sch Med 2, Prague, Czech Republic Carleton Univ, Ottawa, ON, CanadaStraub, Volker论文数: 0 引用数: 0 h-index: 0机构: Newcastle Hosp NHS Fdn Trust, John Walton Mscular Dystrophy Res Ctr, Newcastle Upon Tyne, England Newcastle Univ, Newcastle Upon Tyne, England Carleton Univ, Ottawa, ON, CanadaMengle-Gaw, Laurel论文数: 0 引用数: 0 h-index: 0机构: Camden Grp, St Louis, MO USA Carleton Univ, Ottawa, ON, CanadaSchwartz, Benjamin D.论文数: 0 引用数: 0 h-index: 0机构: Camden Grp, St Louis, MO USA Carleton Univ, Ottawa, ON, CanadaHarper, Amy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Richmond, Richmond, VA USA Carleton Univ, Ottawa, ON, CanadaShieh, Perry B.论文数: 0 引用数: 0 h-index: 0机构: UCLA, Med Sch, Los Angeles, CA USA Carleton Univ, Ottawa, ON, CanadaDe Waele, Liesbeth论文数: 0 引用数: 0 h-index: 0机构: Katholieke Univ Leuven, Dept Dev & Regenerat, Leuven, Belgium Univ Hosp Leuven, Dept Paediat Neurol, Leuven, Belgium Carleton Univ, Ottawa, ON, CanadaCastro, Diana论文数: 0 引用数: 0 h-index: 0机构: UT Southwestern Med Ctr, Dallas, TX USA Carleton Univ, Ottawa, ON, CanadaYang, Michele L.论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Childrens Hosp Colorado, Sch Med, Aurora, CO USA Carleton Univ, Ottawa, ON, CanadaRyan, Monique M.论文数: 0 引用数: 0 h-index: 0机构: Royal Childrens Hosp, Melbourne, Vic, Australia Murdoch Childrens Res Inst, Melbourne, Vic, Australia Carleton Univ, Ottawa, ON, CanadaMcDonald, Craig M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA USA Carleton Univ, Ottawa, ON, CanadaTulinius, Mar论文数: 0 引用数: 0 h-index: 0机构: Queen Silvia Childrens Hosp, Gothenburg, Sweden Carleton Univ, Ottawa, ON, CanadaWebster, Richard I.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Westmead, Kids Neurosci Ctr, Westmead, Australia Carleton Univ, Ottawa, ON, CanadaMcmillan, Hugh J.论文数: 0 引用数: 0 h-index: 0机构: Univ Ottawa, Ottawa, ON, Canada Carleton Univ, Ottawa, ON, CanadaKuntz, Nancy论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp, Chicago, IL USA Carleton Univ, Ottawa, ON, CanadaRao, Vamshi K.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp, Chicago, IL USA Carleton Univ, Ottawa, ON, CanadaBaranello, Giovanni论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Inst Hlth Res, Dubowitz Neuromuscular Ctr, Great Ormond St Inst Child Hlth,Great Ormond St Ho, London, England Carleton Univ, Ottawa, ON, CanadaSpinty, Stefan论文数: 0 引用数: 0 h-index: 0机构: Alder Hey Childrens NHS Fdn Trust, Liverpool, England Carleton Univ, Ottawa, ON, CanadaChilds, Anne-Marie论文数: 0 引用数: 0 h-index: 0机构: Leeds Teaching Hosp Trust, Leeds, England Carleton Univ, Ottawa, ON, CanadaSbrocchi, Annie M.论文数: 0 引用数: 0 h-index: 0机构: Montreal Childrens Hosp, Montreal, PQ, Canada Carleton Univ, Ottawa, ON, CanadaSelby, Kathryn A.论文数: 0 引用数: 0 h-index: 0机构: BC Childrens Hosp Res Inst, Vancouver, BC, Canada Carleton Univ, Ottawa, ON, CanadaMonduy, Migvis论文数: 0 引用数: 0 h-index: 0机构: Nemours Childrens Hosp, Orlando, FL USA Nicklaus Childrens Hosp, Miami, FL USA Carleton Univ, Ottawa, ON, CanadaNevo, Yoram论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Schneider Childrens Med Ctr, Tel Aviv, Israel Carleton Univ, Ottawa, ON, CanadaVilchez, Juan J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Quironsalud Valencia, Valencia, Spain Carleton Univ, Ottawa, ON, CanadaNascimento-Osorio, Andres论文数: 0 引用数: 0 h-index: 0机构: Hosp St Joan de Deu, Inst Recerca Pediat, Neuropaediat Dept, Barcelona, Spain Carleton Univ, Ottawa, ON, CanadaNiks, Erik H.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Dept Neurol, Leiden, Netherlands Carleton Univ, Ottawa, ON, CanadaDe Groot, Imelda J. M.论文数: 0 引用数: 0 h-index: 0机构: Radboud Univ Nijmegen, Med Ctr, Nijmegen, Netherlands Carleton Univ, Ottawa, ON, CanadaKatsalouli, Marina论文数: 0 引用数: 0 h-index: 0机构: PA Kyriakou Childrens Hosp, Athens, Greece Carleton Univ, Ottawa, ON, Canadavan den Anker, John N.论文数: 0 引用数: 0 h-index: 0机构: ReveraGen Biopharm, Rockville, MD 20850 USA Childrens Natl Med Ctr, Washington, DC USA Carleton Univ, Ottawa, ON, CanadaWard, Leanne M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Eastern Ontario CHEO, Res Inst, Ottawa, ON, Canada Carleton Univ, Ottawa, ON, CanadaLeinonen, Mika论文数: 0 引用数: 0 h-index: 0机构: Santhera Pharmaceut, Prattein, Switzerland Carleton Univ, Ottawa, ON, CanadaD'Alessandro, Andrea L.论文数: 0 引用数: 0 h-index: 0机构: TRiNDS, Pittsburgh, PA USA Carleton Univ, Ottawa, ON, CanadaHoffman, Eric P.论文数: 0 引用数: 0 h-index: 0机构: ReveraGen Biopharm, Rockville, MD 20850 USA SUNY Binghamton, Binghamton, NY 13902 USA Carleton Univ, Ottawa, ON, Canada
- [7] Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping A Phase 2 Randomized Clinical TrialJAMA NEUROLOGY, 2020, 77 (08) : 982 - 991Clemens, Paula R.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USA Dept Vet Affairs Med Ctr, Pittsburgh, PA USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USARao, Vamshi K.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Div Neurol, Chicago, IL 60611 USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAConnolly, Anne M.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Nationwide Childrens Hosp, Div Neurol, Columbus, OH 43210 USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAHarper, Amy D.论文数: 0 引用数: 0 h-index: 0机构: Virginia Commonwealth Univ, Childrens Hosp Richmond, Richmond, VA 23284 USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAMah, Jean K.论文数: 0 引用数: 0 h-index: 0机构: Univ Calgary, Dept Pediat, Calgary, AB, Canada Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USASmith, Edward C.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Div Pediat Neurol, Med Ctr, Durham, NC USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAMcDonald, Craig M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, UC Davis Hlth, Dept Pediat, Dept Phys Med & Rehabil, Sacramento, CA 95817 USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAZaidman, Craig M.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Neurol, St Louis, MO 63110 USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAMorgenroth, Lauren P.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Grad Sch Publ Hlth, Pittsburgh, PA USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAOsaki, Hironori论文数: 0 引用数: 0 h-index: 0机构: NS Pharma, Paramus, NJ USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USASatou, Youhei论文数: 0 引用数: 0 h-index: 0机构: NS Pharma, Paramus, NJ USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAYamashita, Taishi论文数: 0 引用数: 0 h-index: 0机构: NS Pharma, Paramus, NJ USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USAHoffman, Eric P.论文数: 0 引用数: 0 h-index: 0机构: Dalhousie Univ, AGADA BioSci, Halifax, NS, Canada SUNY Binghamton, Dept Pharmaceut Sci, Binghamton, NY 13902 USA Univ Pittsburgh, Dept Neurol, Sch Med, 3550 Terrace St, Pittsburgh, PA 15261 USA
- [8] Comparison of brain volume reduction in boys with Duchenne muscular dystrophy treated with different corticosteroid regimesNEUROMUSCULAR DISORDERS, 2022, 32 : S68 - S68Geuens, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Leuven, Belgium Univ Hosp Leuven, Leuven, BelgiumVan Dessel, J.论文数: 0 引用数: 0 h-index: 0机构: Katholieke Univ Leuven, UPC, Leuven, Belgium Univ Hosp Leuven, Leuven, BelgiumLemiere, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Leuven, Belgium Univ Hosp Leuven, Leuven, BelgiumNiks, E.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ Med Ctr, Leiden, Netherlands Univ Hosp Leuven, Leuven, BelgiumGoemans, N.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Leuven, Belgium Univ Hosp Leuven, Leuven, BelgiumKan, H.论文数: 0 引用数: 0 h-index: 0机构: Leidens Univ Med Ctr, Leiden, Netherlands Univ Hosp Leuven, Leuven, BelgiumDe Waele, L.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Leuven, Belgium Univ Hosp Leuven, Leuven, BelgiumDoorenweerd, N.论文数: 0 引用数: 0 h-index: 0机构: Leidens Univ Med Ctr, Leiden, Netherlands Univ Hosp Leuven, Leuven, Belgium
- [9] Vertebral fractures in corticosteroid-treated boys with Duchenne muscular dystrophyNEUROMUSCULAR DISORDERS, 2008, 18 (9-10) : 825 - 826Ambegaonkar, G. P.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, England Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, EnglandKinali, M.论文数: 0 引用数: 0 h-index: 0机构: Inst Child Hlth, Dept Paediat, London, England Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, EnglandMuntoni, F.论文数: 0 引用数: 0 h-index: 0机构: Inst Child Hlth, Dept Paediat, London, England Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, EnglandRobb, S. A.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, England Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, EnglandManzur, A. Y.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, England Great Ormond St Hosp Sick Children, Dept Paediat, London WC1N 3JH, England
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