AAV based gene therapy rescues the murine cardiac phenotype associated with Friedreich ataxia

被引:0
|
作者
Perdomini, Morgane [1 ,2 ]
Belbellaa, Brahim [1 ,2 ]
Monassier, Laurent [3 ]
Cartier, Nathalie [4 ]
Aubourg, Patrick [4 ]
Puccio, Helene [1 ,2 ]
机构
[1] CNRS UMR7104, Inserm U596, Inst Genet & Mol & Cellular Biol, Illkirch Graffenstaden, France
[2] Univ Strasbourg, Illkirch Graffenstaden, France
[3] Fac Med, INSERM E333, Lab Neurobiol & Pharmacol Cardiovasc, Strasbourg, France
[4] INSERM, U745, Paris, France
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
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页码:A43 / A44
页数:2
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