AAV based gene therapy rescues the murine cardiac phenotype associated with Friedreich ataxia

被引：0
|
作者：
Perdomini, Morgane [1 ,2 ]
Belbellaa, Brahim [1 ,2 ]
Monassier, Laurent [3 ]
Cartier, Nathalie [4 ]
Aubourg, Patrick [4 ]
Puccio, Helene [1 ,2 ]
机构：
[1] CNRS UMR7104, Inserm U596, Inst Genet & Mol & Cellular Biol, Illkirch Graffenstaden, France
[2] Univ Strasbourg, Illkirch Graffenstaden, France
[3] Fac Med, INSERM E333, Lab Neurobiol & Pharmacol Cardiovasc, Strasbourg, France
[4] INSERM, U745, Paris, France
来源：
HUMAN GENE THERAPY | 2012年 / 23卷 / 10期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：A43 / A44
页数：2
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