Major tumor regressions in H3K27M-mutated diffuse midline glioma (DMG) following sequential intravenous (IV) and intracerebroventricular (ICV) delivery of GD2-CAR T cells

被引:0
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作者
Majzner, Robbie G. [1 ]
Mahdi, Jasia [1 ]
Ramakrishna, Sneha [1 ]
Patel, Shabnum [1 ]
Chinnasamy, Harshini [1 ]
Yeom, Kristen [1 ]
Schultz, Liora [1 ]
Barsan, Valentin [1 ]
Richards, Rebecca [1 ]
Campen, Cynthia [1 ]
Reschke, Agnes [1 ]
Toland, Angus Martin Shaw [1 ]
Baggott, Christina [1 ]
Mavroukakis, Sharon [1 ]
Egeler, Emily [1 ]
Moon, Jennifer [1 ]
Jacobs, Ashley [1 ]
Yamabe-Kwong, Karen [1 ]
Rasmussen, Lindsey [1 ]
Nie, Esther [1 ]
Green, Sean [1 ]
Kunicki, Michael [1 ]
Fujimoto, Michelle [1 ]
Ehlinger, Zach [1 ]
Reynolds, Warren [1 ]
Prabhu, Snehit [1 ]
Warren, Katherine E. [2 ]
Cornell, Tim [1 ]
Partap, Sonia [1 ]
Fisher, Paul [1 ]
Grant, Gerald [1 ]
Vogel, Hannes [1 ]
Sahaf, Bita [1 ]
Davis, Kara [1 ]
Feldman, Steven [1 ]
Monje, Michelle [1 ]
Mackall, Crystal L. [1 ]
机构
[1] Stanford Univ Sch Med, Stanford, CA USA
[2] Dana Farber Canc Inst, Boston, MA USA
关键词
D O I
暂无
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
CT001
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收藏
页数:2
相关论文
共 24 条
  • [1] MAJOR TUMOR REGRESSIONS IN H3K27M-MUTATED DIFFUSE MIDLINE GLIOMA (DMG) FOLLOWING SEQUENTIAL INTRAVENOUS (IV) AND INTRACEREBROVENTRICULAR (ICV) DELIVERY OF GD2-CAR T-CELLS
    Monje, Michelle
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    Mahdi, Jasia
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    Patel, Shabnum
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    Yeom, Kristen
    Schultz, Liora
    Barsan, Valentin
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    Reschke, Agnes
    Toland, Angus Martin
    Baggott, Christina
    Mavroukakis, Sharon
    Egeler, Emily
    Moon, Jennifer
    Jacobs, Ashley
    Yamabe-Kwong, Karen
    Rasmussen, Lindsey
    Nie, Esther
    Green, Sean
    Kunicki, Michael
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    Ehlinger, Zach
    Reynolds, Warren
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    Warren, Katherine E.
    Cornell, Tim
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    Sahaf, Bita
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    NEURO-ONCOLOGY, 2022, 24 : 20 - 21
  • [2] SEQUENTIAL INTRAVENOUS AND INTRACEREBROVENTRICULAR GD2-CAR T-CELL THERAPY FOR H3K27M-MUTATED DIFFUSE MIDLINE GLIOMAS
    Monje, Michelle
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    Majzner, Robbie G.
    Yeom, Kristen
    Schultz, Liora M.
    Richards, Rebecca
    Barsan, Valentin
    Song, Kun-Wei
    Kamens, Jennifer
    Baggott, Christina
    Kunicki, Michael
    Lim, Alexandria Sung
    Reschke, Agnes
    Mavroukakis, Sharon
    Egeler, Emily
    Moon, Jennifer
    Patel, Shabnum
    Chinnasamy, Harshini
    Erickson, Courtney
    Jacobs, Ashley
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    Fowler, Carley
    Green, Sean
    Beebe, Barbara
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    Brown, Annie Kathleen
    Peterson, Ann-Louise G.
    Mcintyre, Catherine
    Siddiqui, Aman
    Lepori-Bui, Nadia
    Villar, Katlin
    Pham, Kymhuynh
    Bove, Rachel
    Musa, Eric
    Reynolds, Warren
    Kuo, Adam
    Prabhu, Snehit
    Rasmussen, Lindsey
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    NEURO-ONCOLOGY, 2024, 26
  • [3] GD2-CAR T cell therapy for H3K27M-mutated diffuse midline gliomas
    Robbie G. Majzner
    Sneha Ramakrishna
    Kristen W. Yeom
    Shabnum Patel
    Harshini Chinnasamy
    Liora M. Schultz
    Rebecca M. Richards
    Li Jiang
    Valentin Barsan
    Rebecca Mancusi
    Anna C. Geraghty
    Zinaida Good
    Aaron Y. Mochizuki
    Shawn M. Gillespie
    Angus Martin Shaw Toland
    Jasia Mahdi
    Agnes Reschke
    Esther H. Nie
    Isabelle J. Chau
    Maria Caterina Rotiroti
    Christopher W. Mount
    Christina Baggott
    Sharon Mavroukakis
    Emily Egeler
    Jennifer Moon
    Courtney Erickson
    Sean Green
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    Michelle Fujimoto
    Zach Ehlinger
    Warren Reynolds
    Sreevidya Kurra
    Katherine E. Warren
    Snehit Prabhu
    Hannes Vogel
    Lindsey Rasmussen
    Timothy T. Cornell
    Sonia Partap
    Paul G. Fisher
    Cynthia J. Campen
    Mariella G. Filbin
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    Bita Sahaf
    Kara L. Davis
    Steven A. Feldman
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    Nature, 2022, 603 : 934 - 941
  • [4] Intravenous and intracranial GD2-CAR T cells for H3K27M+ diffuse midline gliomas
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    Mahdi, Jasia
    Majzner, Robbie
    Yeom, Kristen W.
    Schultz, Liora M.
    Richards, Rebecca M.
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    Song, Kun-Wei
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    Kunicki, Michael
    Rietberg, Skyler P.
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    Egeler, Emily
    Moon, Jennifer
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    Chinnasamy, Harshini
    Erickson, Courtney
    Jacobs, Ashley
    Duh, Allison K.
    Tunuguntla, Ramya
    Klysz, Dorota Danuta
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    Green, Sean
    Beebe, Barbara
    Carr, Casey
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    Brown, Annie Kathleen
    Petersen, Ann-Louise G.
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    Villar, Katlin
    Pham, Kymhuynh
    Bove, Rachel
    Musa, Eric
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    Partap, Sonia
    Fisher, Paul G.
    Campen, Cynthia J.
    Grant, Gerald
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    NATURE, 2025, 637 (8046) : 708 - 715
  • [5] AVAPRITINIB FOR TARGETING PDGFRA IN H3K27M-MUTATED DIFFUSE MIDLINE GLIOMA
    Mayr, Lisa
    Madlener, Sibylle
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    Baumgartner, Alicia-Christina
    Dorfer, Christian
    Haberler, Christine
    Muellauer, Leonhard
    Palova, Hana
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    Sterba, Jaroslav
    Dieckmann, Karin
    Azizi, Amedeo
    Peyrl, Andreas
    Kim, Sean
    Hsieh, Antony
    Dimitrijevic, Sasa
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    NEURO-ONCOLOGY, 2022, 24 : 32 - 32
  • [6] SIGNIFICANT TUMOR REGRESSION OF H3K27M-MUTATED DIFFUSE MIDLINE GLIOMA OF THE BRAINSTEM WITH PANOBINOSTAT: A CASE REPORT
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  • [7] GD2-CART cell therapy for H3K27M-mutated diffuse midline gliomas
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    Jiang, Li
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    Toland, Angus Martin Shaw
    Mahdi, Jasia
    Reschke, Agnes
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    Chau, Isabelle J.
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    Baggott, Christina
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    Filbin, Mariella G.
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  • [8] GD2-TARGETING CAR T CELLS SHOW PROMISE IN H3K27M-MUTATED GLIOMAS
    不详
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  • [9] GD2 CAR T cells mediate clinical activity and manageable toxicity in children and young adults with DIPG and H3K27M-mutated diffuse midline gliomas.
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