Pitfalls of Drug Development: Lessons Learned from Trials of Denufosol in Cystic Fibrosis

被引：35
|
作者：
Moss, Richard B. [1 ]
机构：
[1] Stanford Univ, Dept Pediat, Sch Med, Stanford, CA 94305 USA
来源：
JOURNAL OF PEDIATRICS | 2013年 / 162卷 / 04期
关键词：
INHALED HYPERTONIC SALINE; P2Y(2) RECEPTOR AGONIST; INHALATION SOLUTION; LUNG-FUNCTION; TETRASODIUM; SAFETY; CLEARANCE; INFANTS; TMEM16A; STRESS;
D O I：
10.1016/j.jpeds.2012.11.034
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
引用
收藏
页码：676 / 680
页数：5
相关论文
共 50 条
  • [1] LESSONS LEARNED FROM THE DENUFOSOL TRIALS
    Moss, Richard B.
    [J]. PEDIATRIC PULMONOLOGY, 2011, : 177 - 178
  • [2] Lessons learned from metabolomics in cystic fibrosis
    Marianne S. Muhlebach
    Wei Sha
    [J]. Molecular and Cellular Pediatrics, 2 (1)
  • [3] Lessons learned from the cystic fibrosis pig
    Meyerholz, David K.
    [J]. THERIOGENOLOGY, 2016, 86 (01) : 427 - 432
  • [4] Cystic Fibrosis Transitions of Care Lessons Learned and Future Directions for Cystic Fibrosis
    Okumura, Megumi J.
    Kleinhenz, Mary Ellen
    [J]. CLINICS IN CHEST MEDICINE, 2016, 37 (01) : 119 - +
  • [5] Lessons learned from 20 years of newborn screening for cystic fibrosis
    Massie, R. John H.
    Curnow, Lisette
    Glazner, Judith
    Armstrong, David S.
    Francis, Ivan
    [J]. MEDICAL JOURNAL OF AUSTRALIA, 2012, 196 (01) : 67 - 70
  • [6] Lessons learned from drug design and development
    Parker, William
    [J]. PERSPECTIVES IN PUBLIC HEALTH, 2016, 136 (04) : 195 - 196
  • [7] Lessons learned from drug trials in neurofibromatosis: A systematic review
    Dhaenens, Britt A. E.
    Ferner, Rosalie E.
    Evans, D. Gareth
    Heimann, Guenter
    Potratz, Cornelia
    van de Ketterij, Edwin
    Kaindl, Angela M.
    Hissink, Geesje
    Carton, Charlotte
    Bakker, Annette
    Nievo, Marco
    Legius, Eric
    Oostenbrink, Rianne
    [J]. EUROPEAN JOURNAL OF MEDICAL GENETICS, 2021, 64 (09)
  • [8] Pediatric Cardiovascular Drug Trials, Lessons Learned
    Li, Jennifer S.
    Cohen-Wolkowiez, Michael
    Pasquali, Sara K.
    [J]. JOURNAL OF CARDIOVASCULAR PHARMACOLOGY, 2011, 58 (01) : 4 - 8
  • [9] Drug development for cystic fibrosis
    Sanders, Don B.
    Chmiel, James F.
    [J]. PEDIATRIC PULMONOLOGY, 2021, 56 : S10 - S22
  • [10] Gene Therapy for Cystic Fibrosis: Lessons Learned and Paths Forward
    Choi, Soon H.
    Engelhardt, John F.
    [J]. MOLECULAR THERAPY, 2021, 29 (02) : 428 - 430
12345