Gene Therapy for Sickle Cell Disease, β-Thalassemia Enters Regulatory Reviews

被引：0
|
作者：
Larkin, Howard D.
机构：
来源：
JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION | 2022年 / 328卷 / 18期
关键词：
D O I：
10.1001/jama.2022.18448
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
[No abstract available]
引用
收藏
页码：1798 / 1798
页数：1
相关论文
共 50 条
  • [1] Gene therapy for sickle cell disease and thalassemia
    Scaramellini, Natalia
    Panzieri, Daniele Lello
    Cappellini, Maria Domenica
    CURRENT OPINION IN HEMATOLOGY, 2025, 32 (03) : 120 - 129
  • [2] Major Challenges for Gene Therapy of Thalassemia and Sickle Cell Disease
    Papanikolaou, Eleni
    Anagnou, Nicholas P.
    CURRENT GENE THERAPY, 2010, 10 (05) : 404 - 412
  • [3] Current status and developments in gene therapy for thalassemia and sickle cell disease
    Yannaki, Evangelia
    Karponi, Garyfalia
    THALASSEMIA REPORTS, 2014, 4 (03) : 75 - 80
  • [4] Gene Therapy for Hemoglobinopathies Beta-Thalassemia, Sickle Cell Disease
    Leonard, Alexis
    Tisdale, John F.
    Bonner, Melissa
    HEMATOLOGY-ONCOLOGY CLINICS OF NORTH AMERICA, 2022, 36 (04) : 769 - 795
  • [5] Bench to Bedside-Gene Therapy for Thalassemia and Sickle Cell Disease
    Leboulch, Philippe
    BLOOD, 2015, 126 (23)
  • [6] Progress toward safe and effective gene therapy for β-thalassemia and sickle cell disease
    Lebensburger, Jeffrey
    Persons, Derek A.
    CURRENT OPINION IN DRUG DISCOVERY & DEVELOPMENT, 2008, 11 (02) : 225 - 232
  • [7] On the road to gene therapy for β-thalassemia and sickle cell anemia
    Bank, Arthur
    PEDIATRIC HEMATOLOGY AND ONCOLOGY, 2008, 25 (01) : 1 - 4
  • [8] Hematopoietic stem cell mobilization strategies for gene therapy of beta thalassemia and sickle cell disease
    Yannaki, Evangelia
    Stamatoyannopoulos, George
    COOLEY'S ANEMIA: NINTH SYMPOSIUM, 2010, 1202 : 59 - 63
  • [9] Hemolytic Anemia Therapy for Thalassemia and Sickle Cell Disease
    Dickerhoff, Roswitha
    DEUTSCHE MEDIZINISCHE WOCHENSCHRIFT, 2015, 140 (22) : 1646 - 1646
  • [10] Gene therapy in the fight against pediatric blood disorders: sickle cell disease and β-thalassemia
    Hu, Wei
    Wang, Bingyuan
    Song, Guowei
    Wang, Xiaojing
    Wang, Xiaoyun
    DRUGS OF THE FUTURE, 2022, 47 (06) : 443 - 456
12345