Efficient mRNA Therapy for Treating Ornithine Transcarbamylase Deficiency in Two Mouse Models

被引：0
|
作者：
Wang, Lili [1 ]
Zhuo, Jenny [2 ]
White, John [1 ]
He, Zhenning [1 ]
Zhang, Hong [1 ]
Bell, Peter [1 ]
Yu, Hongwei [1 ]
Munden, Regina [1 ]
Zimmer, Mike [2 ]
Giangrande, Paloma H. [2 ]
Martini, Paolo [2 ]
Wilson, James M. [1 ]
机构：
[1] Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA
[2] ModernaTX Inc, Cambridge, MA USA
来源：
MOLECULAR THERAPY | 2019年 / 27卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
383
引用
收藏
页码：182 / 182
页数：1
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