iPSC-Based Strategy To Correct the Bleeding Phenotype in Hemophilia A Targeting FVIII Expression to Endothelial Cells

被引：0
|
作者：
Talmon, Maria [1 ]
Ranaldo, Gabriella [1 ]
Grosso, Chantal [1 ]
Lombardo, Angelo [2 ]
Merlin, Simone [1 ]
Cannizzo, Stefania E. [1 ]
Raya, Angel [3 ]
Naldini, Luigi [2 ]
Schinco, Piercarla [4 ]
Follenzi, Antonia [1 ]
机构：
[1] Univ Piemonte Orientale, Dept Hlth Sci, Novara, Italy
[2] H San Raffaele, Tiget, Milan, Italy
[3] Inst Bioengn Catalonia, Barcelona, Spain
[4] Az Osp Univ S Giovanni Battista Molinette, Turin, Italy
来源：
MOLECULAR THERAPY | 2013年 / 21卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
469
引用
收藏
页码：S180 / S180
页数：1
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