CRISPR/Cas9-based gene editing for Rett syndrome therapy

被引:0
|
作者
Croci, S. [1 ,2 ]
Beligni, G. [1 ,2 ]
Rossetti, A. [3 ]
Edo, A. [3 ,12 ]
Sorg, T. [5 ]
Manara, M. [1 ,2 ,6 ]
Lo Rizzo, C. [6 ]
Mencarelli, M. A. [6 ]
Canitano, R. [7 ]
Sica, M. [8 ]
Capitani, K. [1 ,2 ,9 ]
Conticello, S. G. [9 ,10 ]
Molinaro, F. [8 ]
Chiariello, M. [9 ]
Chillon, M. [4 ,11 ,12 ]
Ladewig, J.
Herault, Y. [5 ]
Renieri, A. [1 ,2 ,6 ]
Meloni, I. [1 ,2 ]
机构
[1] Univ Siena, Med Genet, Siena, Italy
[2] Univ Siena, Dept Med Biotechnol, Med Biotech Hub & Competence Ctr, Siena, Italy
[3] Cent Inst Mental Hlth ZI, Dept Translat Brain Res, Mannheim, Germany
[4] Vall dHebron Res Inst VHIR, Barcelona, Spain
[5] CNRS, Inst Clin Souris, ICS, PHENOMIN,MCI,GIE CERBM,IGBMC,CNRS,INSERM, 1 Rue Laurent Fries, F-67404 Illkirch Graffenstaden, France
[6] Azienda Osped Univ Senese, Genet Med, Siena, Italy
[7] Univ Hosp Siena, Div Child & Adolescent Neuropsychiat, Siena, Italy
[8] Univ Siena, S Maria Scotte Hosp, Dept Women & Children, Pediat Surg, Siena, Italy
[9] ISPRO Inst Canc Res Prevent & Clin Network, Core Res Lab, I-50139 Florence, Italy
[10] CNR, Inst Clin Physiol, I-56124 Pisa, Italy
[11] Catalan Inst Res & Adv Studies ICREA, Barcelona, Spain
[12] Univ Barcelona, Inst Neurosci INc, Biochem & Mol Biol Dept, Barcelona, Spain
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
P442
引用
收藏
页码:A141 / A141
页数:1
相关论文
共 50 条
  • [1] Exploration of CRISPR/Cas9-based gene editing as therapy for osteoarthritis
    Zhao, Lan
    Huang, Jian
    Fan, Yunshan
    Li, Jun
    You, Tianming
    He, Shisheng
    Xiao, Guozhi
    Chen, Di
    ANNALS OF THE RHEUMATIC DISEASES, 2019, 78 (05) : 676 - 682
  • [2] CRISPR/Cas9-based Gene Editing in Rice and Maize.
    Yang, Bing
    IN VITRO CELLULAR & DEVELOPMENTAL BIOLOGY-ANIMAL, 2017, 53 : S23 - S23
  • [3] CRISPR/Cas9-based gene activation and base editing in Populus
    Yao, Tao
    Yuan, Guoliang
    Lu, Haiwei
    Liu, Yang
    Zhang, Jin
    Tuskan, Gerald A.
    Muchero, Wellington
    Chen, Jin-Gui
    Yang, Xiaohan
    HORTICULTURE RESEARCH, 2023, 10 (06)
  • [4] Application of CRISPR/Cas9-Based Gene Editing in HIV-1/AIDS Therapy
    Xiao, Qiaoqiao
    Guo, Deyin
    Chen, Shuliang
    FRONTIERS IN CELLULAR AND INFECTION MICROBIOLOGY, 2019, 9
  • [5] CRISPR/Cas9-Based Genome Editing in Plants
    Zhang, Yaling
    Ma, Xingliang
    Xie, Xianrong
    Liu, Yao-Guang
    GENE EDITING IN PLANTS, 2017, 149 : 133 - 150
  • [6] Towards Establishing a CRISPR/Cas9-Based System for Crapemyrtle Gene Editing
    Qin, Hongmin
    HORTSCIENCE, 2023, 58 (09) : S142 - S142
  • [7] Application of the CRISPR/Cas9-based gene editing technique in basic research, diagnosis, and therapy of cancer
    Huimin Zhang
    Chunhong Qin
    Changming An
    Xiwang Zheng
    Shuxin Wen
    Wenjie Chen
    Xianfang Liu
    Zhenghua Lv
    Pingchang Yang
    Wei Xu
    Wei Gao
    Yongyan Wu
    Molecular Cancer, 20
  • [8] Application of the CRISPR/Cas9-based gene editing technique in basic research, diagnosis, and therapy of cancer
    Zhang, Huimin
    Qin, Chunhong
    An, Changming
    Zheng, Xiwang
    Wen, Shuxin
    Chen, Wenjie
    Liu, Xianfang
    Lv, Zhenghua
    Yang, Pingchang
    Xu, Wei
    Gao, Wei
    Wu, Yongyan
    MOLECULAR CANCER, 2021, 20 (01)
  • [9] Delivery systems of CRISPR/Cas9-based cancer gene therapy
    Alessio Biagioni
    Anna Laurenzana
    Francesca Margheri
    Anastasia Chillà
    Gabriella Fibbi
    Mario Del Rosso
    Journal of Biological Engineering, 12
  • [10] Delivery systems of CRISPR/Cas9-based cancer gene therapy
    Biagioni, Alessio
    Laurenzana, Anna
    Margheri, Francesca
    Chilla, Anastasia
    Fibbi, Gabriella
    So, Mario
    JOURNAL OF BIOLOGICAL ENGINEERING, 2018, 12