MUCOPOLYSACCHARIDOSIS TYPE I REPORT OF A SUCCESSFUL HEMATOPOIETIC STEM CELL TRANSPLANTATION AFTER 11 MONTHS OF ENZYME REPLACEMENT THERAPY

被引：0
|
作者：
Bittar, C. M. [1 ]
Vairo, F. [1 ]
Souza, C. F. M. [1 ]
Netto, C. B. [1 ]
Gregianin, L. [2 ]
Galvao, C. [2 ]
Fagondes, S. [3 ]
Giugliani, R. [1 ]
机构：
[1] HCPA, Med Genet Serv, Porto Alegre, RS, Brazil
[2] HCPA, Oncol Serv, Porto Alegre, RS, Brazil
[3] HCPA, Serv Pneumol, Porto Alegre, RS, Brazil
来源：
JOURNAL OF INHERITED METABOLIC DISEASE | 2011年 / 34卷
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D O I：
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中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
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页码：S220 / S220
页数：1
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