Fitusiran Prophylaxis Improves Health-Related Quality of Life in People with Hemophilia a or B, with or without Inhibitors: Results of ATLAS-PPX Study

被引：1

作者：

Kenet, Gili ^{[1
,2
]}

Nolan, Beatrice ^{[3
]}

Matsushita, Tadashi ^{[4
]}

Young, Guy ^{[5
,6
]}

Quan, Ting ^{[7
]}

Cano, Viridiana ^{[8
]}

Sussebach, Christian ^{[9
]}

Andersson, Shauna ^{[8
]}

Mei, Baisong ^{[8
]}

Afonso, Marion ^{[10
]}

Kavakli, Kaan ^{[11
]}

机构：

[1] Tel Aviv Univ, Tel Aviv, Israel

[2] Sheba Med Ctr, Ramat Gan, Israel

[3] Our Ladys Childrens Hosp, Dublin, Ireland

[4] Nagoya Univ Hosp, Dept Transfus Med, Nagoya, Aichi, Japan

[5] Univ Southern Calif, Childrens Hosp Los Angeles, Los Angeles, CA 90007 USA

[6] Univ Southern Calif, Keck Sch Med, Los Angeles, CA 90007 USA

[7] Sanofi, Chengdu, Peoples R China

[8] Sanofi, Cambridge, MA USA

[9] Sanofi, Frankfurt, Germany

[10] Chilly Mazarin, Chilly Mazarin, France

[11] Ege Univ Childrens Hosp, Div Pediat Hematol, Clin Childrens Hlth & Dis, Izmir, Turkey

来源：

BLOOD | 2022年 / 140卷

关键词：

D O I：

10.1182/blood-2022-167169

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：7977 / 7978

页数：2

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