Reduction of Transthyretin Expression by AAV Gene Delivery of a Novel Endonuclease in Mice

被引：0
|
作者：
Greig, Jenny A. [1 ]
Ashley, Scott N. [1 ]
Gorsuch, Cassandra [2 ]
Chorazeczewski, Joanna [1 ]
Furmanak, Thomas [1 ]
Zhu, Yanqing [1 ]
Bell, Peter [1 ]
Sharer, Wendy [2 ]
Li, Hui [2 ]
Smith, Jeff [2 ]
Clark, Peter [1 ]
Breton, Camilo [1 ]
Wilson, James M. [1 ]
机构：
[1] Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA
[2] Precis BioSci, Durham, NC USA
来源：
MOLECULAR THERAPY | 2019年 / 27卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
996
引用
收藏
页码：463 / 463
页数：1
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