Adeno-associated virus-mediated gene transfer of factor IX for treatment of hemophilia B by gene therapy

被引:25
|
作者
Herzog, RW
High, KA
机构
[1] Childrens Hosp Philadelphia, Div Hematol, Abramson Res Ctr 310A, Philadelphia, PA 19104 USA
[2] Univ Penn, Med Ctr, Dept Pediat, Philadelphia, PA 19104 USA
[3] Univ Penn, Med Ctr, Dept Pathol, Philadelphia, PA 19104 USA
关键词
D O I
10.1055/s-0037-1615877
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:540 / 546
页数:7
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