An investigation to determine the efficacy of lentivirus-mediated FXN gene delivery for the correction of Friedreich ataxia

被引：0
|
作者：
Khonsari, Hassan [1 ]
Howe, Steven [2 ]
Waddington, Simon [2 ]
Pook, Mark [1 ]
Themis, Mike [1 ]
机构：
[1] Brunel Univ, London, England
[2] UCL, London, England
来源：
HUMAN GENE THERAPY | 2014年 / 25卷 / 05期
关键词：
Friedreich ataxia; FRDA; Gene Therapy; lentivirus; Frataxin; FXN;
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：A10 / A10
页数：1
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