Pilot Studies of Gene Therapy for Primary Ciliary Dyskinesia

被引:0
|
作者
Ostrowski, L. E.
Yin, W.
Thompson, K. E.
Patel, M.
Olsen, J. C.
机构
关键词
D O I
暂无
中图分类号
R4 [临床医学];
学科分类号
1002 ; 100602 ;
摘要
A6604
引用
收藏
页数:1
相关论文
共 50 条
  • [1] Towards gene therapy for primary ciliary dyskinesia
    Munye, Mustafa M.
    Howe, Steven J.
    Hart, Stephen L.
    HUMAN GENE THERAPY, 2012, 23 (05) : A11 - A11
  • [2] Combined cellular and gene therapy to treat Primary Ciliary Dyskinesia
    Bourdais, C.
    Nasri, A.
    Foisset, F.
    Ahmed, E.
    Vachier, I.
    Bourdin, A.
    Assou, S.
    De Vos, J.
    HUMAN GENE THERAPY, 2022, 33 (23-24) : A159 - A159
  • [3] Quantitative analysis of ciliary beating in primary ciliary dyskinesia: a pilot study
    Papon, Jean-Francois
    Bassinet, Laurence
    Cariou-Patron, Gwenaelle
    Zerah-Lancner, Francoise
    Vojtek, Anne-Marie
    Blanchon, Sylvain
    Crestani, Bruno
    Amselem, Serge
    Coste, Andre
    Housset, Bruno
    Escudier, Estelle
    Louis, Bruno
    ORPHANET JOURNAL OF RARE DISEASES, 2012, 7
  • [4] Quantitative analysis of ciliary beating in primary ciliary dyskinesia: a pilot study
    Jean-François Papon
    Laurence Bassinet
    Gwenaëlle Cariou-Patron
    Francoise Zerah-Lancner
    Anne-Marie Vojtek
    Sylvain Blanchon
    Bruno Crestani
    Serge Amselem
    Andre Coste
    Bruno Housset
    Estelle Escudier
    Bruno Louis
    Orphanet Journal of Rare Diseases, 7
  • [5] Restoring Ciliary Function: Gene Therapeutics for Primary Ciliary Dyskinesia
    Keiser, Nicholas W.
    Cant, Erin
    Sitaraman, Sneha
    Shoemark, Amelia
    Limberis, Maria P.
    HUMAN GENE THERAPY, 2023, 34 (17-18) : 821 - 835
  • [6] Identification of a novel gene for primary ciliary dyskinesia
    Castleman, Victoria
    Chodhar, Rahul
    O'Callaghan, Christopher
    Reish, Orit
    Wallis, Colin
    Gardiner, R. Mark
    Chung, Eddie. M. K.
    Mitchison, Hannah M.
    GENETICS RESEARCH, 2007, 89 (03) : 187 - 187
  • [7] Primary ciliary dyskinesia Review, diagnostics and therapy
    Ahrens, P.
    PNEUMOLOGE, 2012, 9 (03): : 217 - 227
  • [8] Primary ciliary dyskinesia.: Diagnosis and therapy
    Nüsslein, TG
    Rieger, CHL
    MONATSSCHRIFT KINDERHEILKUNDE, 2005, 153 (03) : 255 - 261
  • [9] PRIMARY CILIARY DYSKINESIA
    SLEIGH, MA
    LANCET, 1981, 2 (8244): : 476 - 476
  • [10] Novel Gene Variants Associated with Primary Ciliary Dyskinesia
    Durkadin Demir Eksi
    Elanur Yilmaz
    A. Erdem Basaran
    Gizem Erduran
    Banu Nur
    Ercan Mihci
    Bulent Karadag
    Aysen Bingol
    Ozgul M. Alper
    Indian Journal of Pediatrics, 2022, 89 : 682 - 691