CRITERIA TO DEFINE RARE DISEASES AND ORPHAN DRUGS: SYSTEMATIC LITERATURE REVIEW

被引:0
|
作者
Abozaid, G. [1 ]
Kerr, K. [2 ]
McKnight, A. [2 ]
Al-Omar, H. [3 ]
机构
[1] Princess Nourah bint Abdulrahman Univ, Coll Pharm, Dept Pharm Practice, Riyadh, Saudi Arabia
[2] Queens Univ Belfast, Sch Med Dent & Biomed Sci, Royal Victoria Hosp, Ctr Publ Hlth,Inst Clin Sci B, Belfast, Antrim, North Ireland
[3] King Saud Univ, Coll Pharm, Dept Clin Pharm, Riyadh, Saudi Arabia
关键词
D O I
暂无
中图分类号
F [经济];
学科分类号
02 ;
摘要
HPR173
引用
收藏
页码:S264 / S264
页数:1
相关论文
共 50 条
  • [1] Criteria to define rare diseases and orphan drugs: a systematic review protocol
    Abozaid, Ghada Mohammed
    Kerr, Katie
    McKnight, Amy
    Al-Omar, Hussain A.
    [J]. BMJ OPEN, 2022, 12 (07):
  • [2] VALUE ASSESSMENT OF ORPHAN DRUGS FOR TREATMENT OF RARE DISEASES: A SYSTEMATIC REVIEW
    Lockhart, C. M.
    Hansen, R. N.
    [J]. VALUE IN HEALTH, 2016, 19 (03) : A79 - A79
  • [3] Ethical Questions Linked to Rare Diseases and Orphan Drugs - A Systematic Review
    Kacetl, Jaroslav
    Maresova, Petra
    Maskuriy, Raihan
    Selamat, Ali
    [J]. RISK MANAGEMENT AND HEALTHCARE POLICY, 2020, 13 : 2125 - 2148
  • [4] OF RARE DISEASES AND ORPHAN DRUGS: A REVIEW OF CURRENT NEUROSCIENCE
    Polanco-Carrasco, Roberto
    [J]. PSIENCIA-REVISTA LATINOAMERICANA DE CIENCIA PSICOLOGICA, 2010, 2 (01): : 8 - 14
  • [5] Societal Preferences in Health Technology Assessments for Rare Diseases and Orphan Drugs: A Systematic Literature Review of New Analytic Approaches
    Vasquez, Paola
    Hall, Lisa
    Merlo, Gregory
    [J]. VALUE IN HEALTH REGIONAL ISSUES, 2024, 44
  • [6] Rare diseases and orphan drugs
    Aronson, JK
    [J]. BRITISH JOURNAL OF CLINICAL PHARMACOLOGY, 2006, 61 (03) : 243 - 245
  • [7] Rare diseases and orphan drugs
    Irena Melnikova
    [J]. Nature Reviews Drug Discovery, 2012, 11 : 267 - 268
  • [8] RARE DISEASES AND ORPHAN DRUGS
    DAINA, E
    [J]. LANCET, 1994, 343 (8912): : 1560 - 1561
  • [9] Rare diseases and orphan drugs
    Melnikova, Irena
    [J]. NATURE REVIEWS DRUG DISCOVERY, 2012, 11 (04) : 267 - 268
  • [10] Orphan drugs and rare diseases
    Schulze-Bonhage, Andreas
    Stephani, Ulrich
    [J]. ZEITSCHRIFT FUR EPILEPTOLOGIE, 2019, 32 (04): : 263 - 263