共 50 条
- [1] Gene Therapy with Etranacogene Dezaparvovec for Hemophilia BNEW ENGLAND JOURNAL OF MEDICINE, 2023, 388 (08): : 706 - 718Pipe, S. W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USA Univ Michigan, Dept Pathol, Ann Arbor, MI 48109 USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USALeebeek, F. W. G.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Univ Med Ctr Rotterdam, Med Ctr, Dept Hematol, Rotterdam, Netherlands Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USARecht, M.论文数: 0 引用数: 0 h-index: 0机构: Yale Univ, Sch Med, New Haven, CT USA Amer Thrombosis & Hemostasis Network, Rochester, NY USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAKey, N. S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Med, Chapel Hill, NC USA Univ N Carolina, UNC Blood Res Ctr, Chapel Hill, NC USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USACastaman, G.论文数: 0 引用数: 0 h-index: 0机构: Careggi Univ Hosp, Dept Oncol, Ctr Bleeding Disorders & Coagulat, Florence, Italy Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAMiesbach, W.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Frankfurt, Dept Hemostaseol, Frankfurt, Germany Univ Hosp Frankfurt, Hemophilia Ctr, Med Clin 2, Inst Transfus Med & Immunohematol, Frankfurt, Germany Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USALattimore, S.论文数: 0 引用数: 0 h-index: 0机构: Yale Univ, Sch Med, New Haven, CT USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAPeerlinck, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Dept Vasc Med & Hemostasis, Hemophilia Ctr, Leuven, Belgium Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAVan der Valk, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Utrecht, Univ Med Ctr Utrecht, Van Creveldklin, Utrecht, Netherlands Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USACoppens, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Vasc Med, Med Ctr, Amsterdam, Netherlands Amsterdam Cardiovasc Sci Pulm Hypertens & Thrombo, Amsterdam, Netherlands Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAKampmann, P.论文数: 0 引用数: 0 h-index: 0机构: Rigshop Copenhagen, Dept Hematol, Copenhagen, Denmark Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAMeijer, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAO'Connell, N.论文数: 0 引用数: 0 h-index: 0机构: St James Hosp, Natl Coagulat Ctr, Dublin, Ireland Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAPasi, K. J.论文数: 0 引用数: 0 h-index: 0机构: Queen Mary Univ London, Barts & London Sch Med & Dent, London, England Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAHart, D. P.论文数: 0 引用数: 0 h-index: 0机构: Queen Mary Univ London, Barts & London Sch Med & Dent, London, England Barts Hlth NHS Trust, Royal London Hosp, Haemophilia Ctr, London, England Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAKazmi, R.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Southampton, Southampton, Hants, England Natl Inst Hlth & Care Res, Clin Res Facil, Southampton, Hants, England Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAAstermark, J.论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Dept Translat Med, Lund, Sweden Skane Univ Hosp, Dept Hematol Oncol & Radiat Phys, Malmo, Sweden Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAHermans, C. R. J. R.论文数: 0 引用数: 0 h-index: 0机构: Clin Univ St Luc, Div Hematol, Brussels, Belgium Catholic Univ Louvain, Louvain La Neuve, Belgium Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAKlamroth, R.论文数: 0 引用数: 0 h-index: 0机构: Vivantes Klinikum Friedrichshain, Comprehens Care Hemophilia Treatment Ctr, Berlin, Germany Univ Bonn, Univ Hosp Bonn, Inst Expt Hematol & Transfus Med, Fac Med, Bonn, Germany Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USALemons, R.论文数: 0 引用数: 0 h-index: 0机构: Univ Utah, Dept Pediat, Salt Lake City, UT USA Primary Childrens Med Ctr, Salt Lake City, UT USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAVisweshwar, N.论文数: 0 引用数: 0 h-index: 0机构: Univ S Florida, Tampa, FL USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAvon Drygalski, A.论文数: 0 引用数: 0 h-index: 0机构: Hemophilia & Thrombosis Treatment Ctr, Dept Med, San Diego, CA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Crary, S. E.论文数: 0 引用数: 0 h-index: 0机构: Arkansas Childrens Hosp, Pulaski, AR USA Univ Arkansas Med Sci, Little Rock, AR USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Gomez, E.论文数: 0 引用数: 0 h-index: 0机构: Ctr Inherited Blood Disorders, Orange, CA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAKruse-Jarres, R.论文数: 0 引用数: 0 h-index: 0机构: Washington Ctr Bleeding Disorders, Washington, DC USA Univ Washington, Seattle, WA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAQuon, D. V.论文数: 0 引用数: 0 h-index: 0机构: Luskin Orthopaed Inst Children, Orthopaed Hemophilia Treatment Ctr, Los Angeles, CA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USASymington, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAWang, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Hemophilia & Thrombosis Ctr, Anschutz Med Campus, Aurora, CO USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAWheeler, A. P.论文数: 0 引用数: 0 h-index: 0机构: Vanderbilt Univ, Dept Pathol Microbiol & Immunol, Med Ctr, Nashville, TN USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAGut, R.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USALiu, Y. P.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USADolmetsch, R. E.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USACooper, D. L.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USALi, Y.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAGoldstein, B.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USAMonahan, P. E.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USA
- [2] Hemophilia B and gene therapy: a new chapter with etranacogene dezaparvovecBLOOD ADVANCES, 2024, 8 (07) : 1796 - 1803Anguela, Xavier M.论文数: 0 引用数: 0 h-index: 0机构: Estuary Biotherapeut Inc, Menlo Pk, CA USA Estuary Biotherapeut Inc, Menlo Pk, CA USAHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Rockefeller Univ, 1230 York Ave, New York, NY 10065 USA Univ Penn, Perelman Sch Med, Philadelphia, PA USA Estuary Biotherapeut Inc, Menlo Pk, CA USA
- [3] Etranacogene dezaparvovec-drlb gene therapy for patients with hemophilia B (congenital factor IX deficiency)EXPERT OPINION ON BIOLOGICAL THERAPY, 2023, 23 (12) : 1173 - 1184Sekayan, Tro论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Med, Div Hematol Oncol, San Diego, CA 92093 USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, San Diego, CA 92093 USASimmons, Dana H.论文数: 0 引用数: 0 h-index: 0机构: Capitol Sci, Washington, DC USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, San Diego, CA 92093 USAvon Drygalski, Annette论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Med, Div Hematol Oncol, San Diego, CA 92093 USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, San Diego, CA 92093 USA
- [4] Stable and durable factor IX levels in patients with hemophilia B over 3 years after etranacogene dezaparvovec gene therapyBLOOD ADVANCES, 2023, 7 (19) : 5671 - 5679von Drygalski, Annette论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USAGomez, Esteban论文数: 0 引用数: 0 h-index: 0机构: Ctr Inherited Blood Disorders, Orange, CA USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USAGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Dept Med, Div Hematol Oncol, Sacramento, CA USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USACastaman, Giancarlo论文数: 0 引用数: 0 h-index: 0机构: Careggi Univ Hosp, Ctr Bleeding Disorders, Dept Oncol, Florence, Italy Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USAKey, Nigel S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Med, Div Hematol, Chapel Hill, NC USA Univ N Carolina, Blood Res Ctr, Dept Med, Chapel Hill, NC USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USALattimore, Susan U.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Hemophilia Ctr, Portland, OR USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USALeebeek, Frank W. G.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Dept Hematol, Erasmus MC, Rotterdam, Netherlands Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USAMiesbach, Wolfgang A.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Frankfurt, Inst Transfus Med, Hemophilia Ctr, Med Clin 2, Frankfurt, Germany Univ Hosp Frankfurt, Inst Transfus Med, Dept Hemostaseol, Med Clin 2, Frankfurt, Germany Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USARecht, Michael论文数: 0 引用数: 0 h-index: 0机构: American Thrombosis & Hemostasis Network, Rochester, NY USA Yale Univ, Hemophilia Treatment Ctr, Sch Med, New Haven, CT USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USAGut, Robert论文数: 0 引用数: 0 h-index: 0机构: UniQure Inc, Lexington, MA USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USADolmetsch, Ricardo论文数: 0 引用数: 0 h-index: 0机构: UniQure Inc, Lexington, MA USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USAMonahan, Paul E.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USALe Quellec, Sandra论文数: 0 引用数: 0 h-index: 0机构: CSL Behring Europe, Hattersheim, Germany Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USAPipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI USA Univ Michigan, Dept Pathol, Ann Arbor, MI USA Univ Calif San Diego, Dept Med, Div Hematol Oncol, 9333 Genesse Ave,Suite 310, San Diego, CA 92121 USA
- [5] MULTIPLE-YEAR DURABILITY DATA FROM A PHASE 2B TRIAL OF GENE THERAPY WITH ETRANACOGENE DEZAPARVOVEC IN PATIENTS WITH HEMOPHILIA BHAEMOPHILIA, 2022, 28 : 74 - 75Gomez, E.论文数: 0 引用数: 0 h-index: 0机构: Phoenix Childrens Hosp, Phoenix, AZ USA Phoenix Childrens Hosp, Phoenix, AZ USACastaman, G.论文数: 0 引用数: 0 h-index: 0机构: Azienda Osped Univ Careggi, Florence, Italy Phoenix Childrens Hosp, Phoenix, AZ USAKey, N. S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC 27515 USA Phoenix Childrens Hosp, Phoenix, AZ USALattimore, S. U.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Portland, OR 97201 USA Phoenix Childrens Hosp, Phoenix, AZ USALeebeek, F. W.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Phoenix Childrens Hosp, Phoenix, AZ USAMiesbach, W. A.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Frankfurt, Frankfurt, Germany Phoenix Childrens Hosp, Phoenix, AZ USA论文数: 引用数: h-index:机构:von Drygalski, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA 92093 USA Phoenix Childrens Hosp, Phoenix, AZ USACooper, D.论文数: 0 引用数: 0 h-index: 0机构: uniQure BV, Amsterdam, Netherlands uniQure Inc, Lexington, MA USA Phoenix Childrens Hosp, Phoenix, AZ USALi, Y.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Phoenix Childrens Hosp, Phoenix, AZ USASalazar, B.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Phoenix Childrens Hosp, Phoenix, AZ USAPipe, S. W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI 48109 USA Phoenix Childrens Hosp, Phoenix, AZ USA
- [6] MULTIPLE-YEAR DURABILITY DATA FROM A PHASE 2B TRIAL OF GENE THERAPY WITH ETRANACOGENE DEZAPARVOVEC IN PATIENTS WITH HEMOPHILIA BAMERICAN JOURNAL OF HEMATOLOGY, 2023, 98 : E41 - E42Gomez, Esteban论文数: 0 引用数: 0 h-index: 0机构: Phoenix Childrens Hosp, Phoenix, AZ USA Phoenix Childrens Hosp, Phoenix, AZ USAGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA USA Phoenix Childrens Hosp, Phoenix, AZ USACastaman, Giancarlo论文数: 0 引用数: 0 h-index: 0机构: Azienda Osped Univ Careggi, Florence, Italy Phoenix Childrens Hosp, Phoenix, AZ USAKey, Nigel S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC USA Phoenix Childrens Hosp, Phoenix, AZ USA论文数: 引用数: h-index:机构:Leebeek, Frank W. G.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Phoenix Childrens Hosp, Phoenix, AZ USAMiesbach, Wolfgang A.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Frankfurt, Frankfurt, Germany Phoenix Childrens Hosp, Phoenix, AZ USA论文数: 引用数: h-index:机构:von Drygalski, Annette论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA USA Phoenix Childrens Hosp, Phoenix, AZ USACooper, David论文数: 0 引用数: 0 h-index: 0机构: uniQure BV, Amsterdam, Netherlands uniQure Inc, Lexington, MA USA Phoenix Childrens Hosp, Phoenix, AZ USALi, Yanyan论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Phoenix Childrens Hosp, Phoenix, AZ USASalazar, Blanca论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA Phoenix Childrens Hosp, Phoenix, AZ USAPipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI USA Phoenix Childrens Hosp, Phoenix, AZ USA
- [7] EFFICACY AND SAFETY OF ETRANACOGENE DEZAPARVOVEC IN ADULTS WITH SEVERE OR MODERATE-SEVERE HEMOPHILIA B: FIRST DATA FROM THE PHASE 3 HOPE-B GENE THERAPY TRIALHAEMOPHILIA, 2021, 27 : 65 - 66Pipe, S. W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI 48109 USA Univ Michigan, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Key, N. S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC 27515 USA Univ Michigan, Ann Arbor, MI 48109 USALeebeek, F. W. G.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Univ Michigan, Ann Arbor, MI 48109 USACastaman, G.论文数: 0 引用数: 0 h-index: 0机构: Azienda Osped Univ Careggi, Florence, Italy Univ Michigan, Ann Arbor, MI 48109 USALattimore, S. U.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Portland, OR 97201 USA Univ Michigan, Ann Arbor, MI 48109 USAvan der Valk, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Utrecht, Van Creveldklin, Utrecht, Netherlands Univ Michigan, Ann Arbor, MI 48109 USAPeerlinck, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Leuven, Belgium Univ Michigan, Ann Arbor, MI 48109 USACoppens, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam Univ Med Ctr, Amsterdam, Netherlands Univ Michigan, Ann Arbor, MI 48109 USAO'Connell, N.论文数: 0 引用数: 0 h-index: 0机构: St James Hosp, Dublin, Ireland Univ Michigan, Ann Arbor, MI 48109 USAPasi, K. J.论文数: 0 引用数: 0 h-index: 0机构: Barts & London Queen Marys Sch Med & Dent, Royal London Haemophilia Ctr, London, England Univ Michigan, Ann Arbor, MI 48109 USAKampmann, P.论文数: 0 引用数: 0 h-index: 0机构: Rigshosp, Copenhagen, Denmark Univ Michigan, Ann Arbor, MI 48109 USAMeijer, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Groningen, Groningen, Netherlands Univ Michigan, Ann Arbor, MI 48109 USAvon Drygalski, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, La Jolla, CA 92093 USA Univ Michigan, Ann Arbor, MI 48109 USAYoung, G.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA 90027 USA Univ Michigan, Ann Arbor, MI 48109 USAHermans, C.论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, Clin Univ St Luc, Brussels, Belgium Univ Michigan, Ann Arbor, MI 48109 USAAstermark, J.论文数: 0 引用数: 0 h-index: 0机构: Skane Univ Hosp, Malmo, Sweden Univ Michigan, Ann Arbor, MI 48109 USAKlamroth, R.论文数: 0 引用数: 0 h-index: 0机构: Vivantes Klinikum Friedrichshain, Berlin, Germany Univ Michigan, Ann Arbor, MI 48109 USALemons, R. S.论文数: 0 引用数: 0 h-index: 0机构: Univ Utah, Salt Lake City, UT USA Univ Michigan, Ann Arbor, MI 48109 USAVisweshwar, N.论文数: 0 引用数: 0 h-index: 0机构: Univ S Florida, Tampa, FL 33620 USA Univ Michigan, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Kazmi, R.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Southampton NHS Fdn Trust, Southampton, Hants, England Univ Michigan, Ann Arbor, MI 48109 USASymington, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Cambridge, Addenbrookes Hosp, Cambridge, England Univ Michigan, Ann Arbor, MI 48109 USAEscobar, M. A.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Hlth Sci Ctr Houston, Houston, TX 77030 USA Univ Michigan, Ann Arbor, MI 48109 USAGomez, E.论文数: 0 引用数: 0 h-index: 0机构: Phoenix Childrens Hosp, Phoenix, AZ USA Univ Michigan, Ann Arbor, MI 48109 USAKruse-Jarres, R.论文数: 0 引用数: 0 h-index: 0机构: BloodWorks NorthWest, Seattle, WA USA Univ Michigan, Ann Arbor, MI 48109 USAKotowski, A.论文数: 0 引用数: 0 h-index: 0机构: Hemophilia Ctr Western New York, New York, NY USA Univ Michigan, Ann Arbor, MI 48109 USAQuon, D.论文数: 0 引用数: 0 h-index: 0机构: Los Angeles Orthoped Hosp, Orthoped Hemophilia Treatment Ctr, Los Angeles, CA USA Univ Michigan, Ann Arbor, MI 48109 USAWang, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Anschutz Med Campus, Aurora, CO USA Univ Michigan, Ann Arbor, MI 48109 USAWheeler, A. P.论文数: 0 引用数: 0 h-index: 0机构: Vanderbilt Univ, Med Ctr, Nashville, TN USA Univ Michigan, Ann Arbor, MI 48109 USASawyer, E. K.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Ann Arbor, MI 48109 USAVerweij, S.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Ann Arbor, MI 48109 USAColletta, V.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Ann Arbor, MI 48109 USABajwa, N.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Ann Arbor, MI 48109 USAGut, R.论文数: 0 引用数: 0 h-index: 0机构: UniQure, Lexington, MA USA Univ Michigan, Ann Arbor, MI 48109 USAMiesbach, W.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Frankfurt, Frankfurt, Germany Univ Michigan, Ann Arbor, MI 48109 USA
- [8] Comprehensive analysis and prediction of long-term durability of factor IX activity following etranacogene dezaparvovec gene therapy in the treatment of hemophilia BCURRENT MEDICAL RESEARCH AND OPINION, 2023, 39 (02) : 227 - 237Shah, Jinesh论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USAKim, Hongseok论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USASivamurthy, Krupa论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USAMonahan, Paul E.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USAFries, Michael论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USA
- [9] MANAGEMENT OF DENTAL PROCEDURES AND SURGERIES IN PEOPLE WITH SEVERE AND MODERATELY SEVERE HAEMOPHILIA B WHO WERE TREATED IN GENE THERAPY CLINICAL TRIALS WITH ETRANACOGENE DEZAPARVOVECHAEMOPHILIA, 2023, 29 : 18 - 19O'Connell, N.论文数: 0 引用数: 0 h-index: 0机构: St James Hosp, Natl Coagulat Ctr, Dublin, Ireland St James Hosp, Natl Coagulat Ctr, Dublin, IrelandVan der Valk, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Utrecht, Univ Med Ctr Utrecht, Dept Benign Hematol, Van Creveldklin, Utrecht, Netherlands St James Hosp, Natl Coagulat Ctr, Dublin, IrelandGomez, E.论文数: 0 引用数: 0 h-index: 0机构: Ctr Inherited Blood Disorders, Orange, CA USA St James Hosp, Natl Coagulat Ctr, Dublin, IrelandMonahan, P. E.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA St James Hosp, Natl Coagulat Ctr, Dublin, IrelandLe Quellec, S.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring Europe, Hattersheim am Main, Germany St James Hosp, Natl Coagulat Ctr, Dublin, IrelandKampmann, P.论文数: 0 引用数: 0 h-index: 0机构: Rigshosp, Dept Hematol, Copenhagen, Denmark St James Hosp, Natl Coagulat Ctr, Dublin, Ireland
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