Regulated Expression of GATA1 as a Gene Therapy Cure for Diamond-Blackfan Anemia

被引：0
|
作者：
Voit, Richard A. [1 ,2 ,3 ]
Liao, Xiaotian [1 ,3 ]
Cohen, Blake [1 ,3 ]
Armant, Myriam A. [4 ]
Kamal, Elena [1 ,3 ]
Huang, Mei-Mei [1 ]
Duncan, Christine [2 ]
Shimamura, Akiko [1 ]
Williams, David A. [1 ]
Sankaran, Vijay G. [1 ,2 ,3 ]
机构：
[1] Boston Childrens Hosp, Div Hematol, Boston, MA USA
[2] Dana Farber Childrens Hosp Canc Ctr, Boston, MA USA
[3] Broad Inst, Cambridge, MA USA
[4] Boston Childrens Hosp, Boston, MA USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
635
引用
收藏
页码：318 / 319
页数：2
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