Development of an AAV Gene Therapy for Hereditary Spastic Paraplegia Type 4 (SPG4-HSP)

被引：0

作者：

Hall, Erin F. ^{[1
]}

Gallagher, Jillian ^{[1
]}

Taghian, Toloo ^{[1
]}

McElroy, Abby ^{[1
]}

Benatti, Hector Ribeiro ^{[1
]}

Prestigiacomo, Rachel ^{[1
]}

Bertrand, Stephanie ^{[2
]}

Piermarini, Emanuela ^{[3
]}

Qiang, Liang ^{[3
]}

Baas, Peter ^{[3
]}

Sena-Esteves, Miguel ^{[1
]}

Gray-Edwards, Heather L. ^{[1
]}

机构：

[1] Univ Massachusetts, Horae Gene Therapy Ctr, Chan Med Sch, Worcester, MA USA

[2] Tufts Univ, Cummings Sch Vet Med, North Grafton, MA USA

[3] Drexel Univ, Dept Neurobiol Anat, Coll Med, Philadelphia, PA USA

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

703

引用

页码：350 / 351

页数：2

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