Hemophilia A Gene Therapy - Some Answers, More Questions

被引：8

|

作者：

George, Lindsey A. ^{[1
,2
,3
]}

机构：

[1] Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA

[2] Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA

[3] Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

来源：

NEW ENGLAND JOURNAL OF MEDICINE | 2023年 / 388卷 / 08期

关键词：

VALOCTOCOGENE ROXAPARVOVEC;

D O I：

10.1056/NEJMe2212347

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

收藏

页码：761 / 763

页数：3

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