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- [1] Severity and burden of sickle cell disease in France: a nationwide real-world studyREVISTA CHILENA DE LITERATURA, 2022, (108): : 2476 - 2486Brousse, Valentine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, France Univ Antilles, INSERM, BIGR, Paris, France Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, FranceBernaudin, Francoise论文数: 0 引用数: 0 h-index: 0机构: DrepaGreffe Assoc, SFGM TC Soc Francaise Greffe Moelle & Therapie Cel, French Referral Ctr Sickle Cell Dis, Nogent Sur Marne, France Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, FranceMelaine, Asma论文数: 0 引用数: 0 h-index: 0机构: Steve Consultants, Oullins, France Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, FranceGoguillot, Melanie论文数: 0 引用数: 0 h-index: 0机构: Steve Consultants, Oullins, France Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, FranceGallagher, Meghan论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Somerville, MA USA Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, FranceBenard, Steve论文数: 0 引用数: 0 h-index: 0机构: Steve Consultants, Oullins, France Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, FranceHabibi, Anoosha论文数: 0 引用数: 0 h-index: 0机构: Paris Est Creteil Univ, Henri Mondor Hosp, AP HP, INSERM Unit 955,Lab Excellence GR Ex,Mondor Inst B, Creteil, Paris, France Univ Paris Cite, Hop Robert Debre, AP-HP, Serv Hematol Immunol,Ctr Reference MCGRE, Paris, France
- [2] Severity and burden of sickle cell disease in France: a nationwide real-world studyHAEMATOLOGICA, 2023, 108 (09) : 2476 - 2486Brousse, Valentine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, France Univ Antilles, INSERM, BIGR, Paris, France Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, FranceBernaudin, Francoise论文数: 0 引用数: 0 h-index: 0机构: DrepaGreffe Assoc, French Referral Ctr Sickle Cell Dis, SFGM TC, Nogent Sur Marne, France Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, FranceMelaine, Asma论文数: 0 引用数: 0 h-index: 0机构: Steve Consultants, Oullins, France Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, FranceGoguillot, Melanie论文数: 0 引用数: 0 h-index: 0机构: Steve Consultants, Oullins, France Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, FranceGallagher, Meghan论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio Inc, Somerville, MA USA Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, FranceBenard, Steve论文数: 0 引用数: 0 h-index: 0机构: Steve Consultants, Oullins, France Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, FranceHabibi, Anoosha论文数: 0 引用数: 0 h-index: 0机构: Paris Est Creteil Univ, Mondor Inst Biomed Res, Henri Mondor Hosp,Lab Excellence GR Ex, AP HP,UPEC,INSERM Unit 955,Sickle Cell Referral C, Creteil, France Univ Paris Cite, Ctr Reference MCGRE, Serv Hematol Immunol, Hop Robert Debre,AP HP, Paris, France
- [3] Sickle Cell Disease (SCD) Burden on Patients Treated With Hydroxyurea (HU): Results from the Real-World Assessment Survey for SCD in Saudi (ROARS)BLOOD, 2022, 140 : 10879 - 10880Ezzat, Hatoon M.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAl Zayed, Abdullah Hasan论文数: 0 引用数: 0 h-index: 0机构: Qatif Cent Hosp, Qatif, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAl Saeed, Hussain H.论文数: 0 引用数: 0 h-index: 0机构: Qatif Cent Hosp, Qatif, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAl Darwish, Mohamed论文数: 0 引用数: 0 h-index: 0机构: Qatif Cent Hosp, Qatif, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAlbagshi, Muneer论文数: 0 引用数: 0 h-index: 0机构: Almana Gen Hosp Al Ahsa, Hofouf, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaMalhan, Hafiz论文数: 0 引用数: 0 h-index: 0机构: Prince Mohamed Bin Naser, Jizan, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaTarawah, Ahmad论文数: 0 引用数: 0 h-index: 0机构: King Salman Med City Al Madinah, Madinah, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAl Manea, Aljawhara论文数: 0 引用数: 0 h-index: 0机构: King Fahad Armed Forces Hosp, Jeddah, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAlhazmi, Iman论文数: 0 引用数: 0 h-index: 0机构: King Fahad Armed Forces Hosp, Jeddah, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaQari, Mohamed论文数: 0 引用数: 0 h-index: 0机构: King Abdulaziz Univ Hosp, Jeddah, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAlzahrani, Azzah论文数: 0 引用数: 0 h-index: 0机构: Prince Sultan Mil Med City, Riyadh, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAlzahrani, Mohsen论文数: 0 引用数: 0 h-index: 0机构: King Abdul Aziz Med City, Riyadh, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaSoliman, Wesam论文数: 0 引用数: 0 h-index: 0机构: Novartis Saudi Ltd, Riyadh, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaAskar, Farid论文数: 0 引用数: 0 h-index: 0机构: Novartis Saudi Ltd, Riyadh, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaYassin, Al Shaimaa论文数: 0 引用数: 0 h-index: 0机构: Novartis Saudi Ltd, Riyadh, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi ArabiaJastaniah, Wasil论文数: 0 引用数: 0 h-index: 0机构: King Faisal Specialist Hosp & Res Ctr Gen Org, Jeddah, Saudi Arabia Johns Hopkins Aramco Healthcare, MOH, Dhahran, Saudi Arabia
- [4] Real-World Evidence on Disease Burden and Economic Impact of Sickle Cell Disease in ItalyJOURNAL OF CLINICAL MEDICINE, 2023, 12 (01)De Franceschi, Lucia论文数: 0 引用数: 0 h-index: 0机构: Univ Verona, Dept Med, I-37129 Verona, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyCastiglioni, Chiara论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, I-20154 Milan, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyCondorelli, Claudia论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, I-20154 Milan, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyValsecchi, Diletta论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, I-20154 Milan, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyPremoli, Eleonora论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, I-20154 Milan, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyFiocchi, Carina论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, I-20154 Milan, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyPerrone, Valentina论文数: 0 引用数: 0 h-index: 0机构: CliCon Srl, Soc Benefit Hlth Econ & Outcomes Res, I-40137 Bologna, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyEsposti, Luca Degli论文数: 0 引用数: 0 h-index: 0机构: CliCon Srl, Soc Benefit Hlth Econ & Outcomes Res, I-40137 Bologna, Italy Univ Verona, Dept Med, I-37129 Verona, ItalyForni, Gian Luca论文数: 0 引用数: 0 h-index: 0机构: Osped Galliera, Ctr Microcitemia & Anemie Congenite, I-16128 Genoa, Italy Univ Verona, Dept Med, I-37129 Verona, Italy
- [5] The Increased Burden of Sickle Cell Disease in Italy: Findings from the Greatalys (Generating Real world Evidence Across ITALy In SCD) StudyBLOOD, 2021, 138 : 1950 - +Franceschi, Luciade论文数: 0 引用数: 0 h-index: 0机构: Univ Verona, Dept Med, Policlinico GB Rossi, Verona, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyForni, Gian Luca论文数: 0 引用数: 0 h-index: 0机构: Osped Galliera, Ctr Microcitemia, Genoa, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyCastiglioni, Chiara论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, Origgio, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyCondorelli, Claudia论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, Origgio, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyValsecchi, Diletta论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, Origgio, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyPremoli, Eleonora论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, Origgio, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyPerrone, Valentina论文数: 0 引用数: 0 h-index: 0机构: Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyDegli Esposti, Luca论文数: 0 引用数: 0 h-index: 0机构: CliCon srl, Hlth Econ Outcomes Res, Bologna, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, ItalyFiocchi, Carina Andrea论文数: 0 引用数: 0 h-index: 0机构: Novartis Farma SpA, Origgio, Italy Univ Verona, Dept Med, Policlinico GB Rossi, Verona, Italy
- [6] Epidemiology and disease burden of sickle cell disease in France: A descriptive study based on a French nationwide claim databasePLOS ONE, 2021, 16 (07):Leleu, Henri论文数: 0 引用数: 0 h-index: 0机构: Publ Hlth Expertise, Paris, France Publ Hlth Expertise, Paris, FranceArlet, Jean Benoit论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Georges Pompidou European Hosp, Sickle Cell Dis Natl Referral Ctr, Internal Med Dept, Paris, France Publ Hlth Expertise, Paris, FranceHabibi, Anoosha论文数: 0 引用数: 0 h-index: 0机构: Henri Mondor Hosp, Sickle Cell Referral Ctr, Internal Med Unit, IMRB Team 2,UPEC,Labex GRex, Creteil, France Publ Hlth Expertise, Paris, FranceEtienne-Julan, Maryse论文数: 0 引用数: 0 h-index: 0机构: Antilles Univ, Pointe A Pitre Hosp, Referral Ctr Sickle Cell Dis, Pointe A Pitre, Guadeloupe, France Publ Hlth Expertise, Paris, FranceKhellaf, Mehdi论文数: 0 引用数: 0 h-index: 0机构: Paris Est Univ, Henri Mondor Hosp, AP HP, INSERM,U955,Emergency Dept, Creteil, France Publ Hlth Expertise, Paris, FranceAdjibi, Yolande论文数: 0 引用数: 0 h-index: 0机构: Henri Mondor Hosp, FMDT Sos Globi, Creteil, France Publ Hlth Expertise, Paris, FrancePirenne, France论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Est Creteil, Fac Med Creteil, Etab Francais du Sang EFS, Creteil, France INSERM, U955, Lab Excellence GRex, Creteil, France Publ Hlth Expertise, Paris, FrancePitel, Marine论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Paris, France Publ Hlth Expertise, Paris, FranceGranghaud, Anna论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Paris, France Publ Hlth Expertise, Paris, FranceSinniah, Cynthia论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Paris, France Publ Hlth Expertise, Paris, FranceDe Montalembert, Mariane论文数: 0 引用数: 0 h-index: 0机构: Necker Hosp Sick Children, Reference Ctr Sickle Cell Dis, Dept Gen Pediat & Pediat Infect Dis, Paris, France Publ Hlth Expertise, Paris, FranceGalacteros, Frederic论文数: 0 引用数: 0 h-index: 0机构: Henri Mondor Hosp, Sickle Cell Referral Ctr, Internal Med Unit, IMRB Team 2,UPEC,Labex GRex, Creteil, France Publ Hlth Expertise, Paris, France
- [7] Real-world evidence of the burden of sickle cell disease: a 5-year longitudinal study at a Brazilian reference centerHEMATOLOGY TRANSFUSION AND CELL THERAPY, 2024, 46 (02) : 161 - 166Barros, Gisele dos Santos论文数: 0 引用数: 0 h-index: 0机构: Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, Brazil Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, BrazilLeal, Carla Vaneska Fernandes论文数: 0 引用数: 0 h-index: 0机构: Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, Brazil Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, BrazilLeite, Lauro Augusto Caetano论文数: 0 引用数: 0 h-index: 0机构: Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, Brazil Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, BrazilFujimoto, Denys Eiti论文数: 0 引用数: 0 h-index: 0机构: Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, Brazil Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, BrazilCancado, Rodolfo Delfini论文数: 0 引用数: 0 h-index: 0机构: Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, Brazil Fac Ciencias Med Santa Casa Sao Paulo, Rua Marques de Itu,579, Sao Paulo, SP, Brazil
- [8] Sickle Cell Disease Mortality in Brazil: Real-World EvidenceBLOOD, 2021, 138Cancado, Rodolfo D.论文数: 0 引用数: 0 h-index: 0机构: Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, BrazilCosta, Fernando Ferreira论文数: 0 引用数: 0 h-index: 0机构: Univ Estadual Campinas, Sch Med Sci, Campinas, SP, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, BrazilLobo, Clarisse论文数: 0 引用数: 0 h-index: 0机构: Inst Estadual Hematol Arthur Siqueira Cavalca, Rio De Janeiro, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, BrazilMigliavaca, Celina Borges论文数: 0 引用数: 0 h-index: 0机构: HT Analyze Consultoria & Treinamento, Porto Alegre, RS, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, BrazilFalavigna, Maicon论文数: 0 引用数: 0 h-index: 0机构: HT Analyze Consultoria & Treinamento, Porto Alegre, RS, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, BrazilSouza Filho, Homero C. R.论文数: 0 引用数: 0 h-index: 0机构: Novartis Oncol, Dept Hematol Oncol, Sao Paulo, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, BrazilBueno, Carolina Tosin论文数: 0 引用数: 0 h-index: 0机构: Novartis Oncol, Sao Paulo, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, BrazilSilva Pinto, Ana Cristina论文数: 0 引用数: 0 h-index: 0机构: Univ Sao Paulo, Ribeirao Preto Med Sch, Blood Ctr Ribeirao Preto, Ribeirao Preto, Brazil Santa Casa Med Sch, Dept Hematol Oncol, Sao Paulo, Brazil
- [9] Real-World effectiveness of voxelotor for the treatment of sickle cell diseaseBRITISH JOURNAL OF HAEMATOLOGY, 2023, 201 : 118 - 118Barcelos, Giovanna论文数: 0 引用数: 0 h-index: 0机构: Global Blood Therapeut Inc, San Francisco, CA USA Global Blood Therapeut Inc, San Francisco, CA USA论文数: 引用数: h-index:机构:Lipato, Thokozeni论文数: 0 引用数: 0 h-index: 0机构: VCU Hlth, Richmond, VA USA Global Blood Therapeut Inc, San Francisco, CA USADelea, Thomas E.论文数: 0 引用数: 0 h-index: 0机构: PAI, Brookline, MA USA Global Blood Therapeut Inc, San Francisco, CA USALonshteyn, Alexander论文数: 0 引用数: 0 h-index: 0机构: PAI, Brookline, MA USA Global Blood Therapeut Inc, San Francisco, CA USAWeycker, Derek论文数: 0 引用数: 0 h-index: 0机构: PAI, Brookline, MA USA Global Blood Therapeut Inc, San Francisco, CA USANguyen, Andy论文数: 0 引用数: 0 h-index: 0机构: Global Blood Therapeut Inc, San Francisco, CA USA Global Blood Therapeut Inc, San Francisco, CA USABeaubrun, Anne论文数: 0 引用数: 0 h-index: 0机构: Global Blood Therapeut Inc, San Francisco, CA USA Global Blood Therapeut Inc, San Francisco, CA USA论文数: 引用数: h-index:机构:
- [10] Real-World Effectiveness of Osteoporosis Medications in France: A Nationwide Cohort StudyJBMR PLUS, 2023, 7 (09)Bosco-Levy, Pauline论文数: 0 引用数: 0 h-index: 0机构: Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France Univ Bordeaux, Bordeaux PharmacoEpi BPE, CHU Bordeaux Adera, CIC 1401, Batiment Le Tondu Case 41,146 Rue Leo Saignat, F-33076 Bordeaux, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, FranceBriot, Karine论文数: 0 引用数: 0 h-index: 0机构: Hop Cochin, Serv Rhumatol, Paris, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, FranceMehsen-Cetre, Nadia论文数: 0 引用数: 0 h-index: 0机构: CHU Pellegrin Tripode, Serv Rhumatol, Bordeaux, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, FranceO'Kelly, James论文数: 0 引用数: 0 h-index: 0机构: Amgen Ltd, Cambridge, England Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, FranceDesamericq, Gaelle论文数: 0 引用数: 0 h-index: 0机构: Amgen SAS, Boulogne Billancourt, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, FranceAbouelfath, Abdelilah论文数: 0 引用数: 0 h-index: 0机构: Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, FranceLassalle, Regis论文数: 0 引用数: 0 h-index: 0机构: Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France论文数: 引用数: h-index:机构:Grolleau, Adeline论文数: 0 引用数: 0 h-index: 0机构: Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France论文数: 引用数: h-index:机构:Droz-Perroteau, Cecile论文数: 0 引用数: 0 h-index: 0机构: Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France Univ Bordeaux, Bordeaux PharmacoEpi, INSERM, CIC P 1401, Bordeaux, France