The Phase 3 RESILIENT Study: Taldefgrobep Alfa in Spinal Muscular Atrophy

被引：0
|
作者：
Lair, L. [1 ]
Qureshi, I. [1 ]
Bechtold, C. [1 ]
Durham, S. [1 ]
Campbell, D. [1 ]
Marin, J. [1 ]
Coric, V. [1 ]
机构：
[1] Biohaven Pharmaceut Inc, New Haven, CT USA
来源：
EUROPEAN JOURNAL OF NEUROLOGY | 2023年 / 30卷
关键词：
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
EPO-199
引用
收藏
页码：448 / 448
页数：1
相关论文
共 50 条
  • [1] Taldefgrobep Alfa and the Phase 3 RESILIENT Trial in Spinal Muscular Atrophy
    Servais, Laurent
    Lair, Lindsey Lee
    Connolly, Anne M.
    Byrne, Barry J.
    Chen, Karen S.
    Coric, Vlad
    Qureshi, Irfan
    Durham, Susan
    Campbell, Daniel J.
    Maclaine, Grant
    Marin, Jackie
    Bechtold, Clifford
    INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2024, 25 (19)
  • [2] Taldefgrobep alfa: preclinical and clinical data supporting the phase 3 RESILIENT study in spinal muscular atrophy
    Lair, L.
    Qureshi, I.
    Bechtold, C.
    Heller, L.
    Durham, S.
    Campbell, D.
    Marin, J.
    Chen, K.
    Coric, V.
    NEUROMUSCULAR DISORDERS, 2023, 33 : S163 - S163
  • [3] AVXS-101 PHASE 3 STUDY IN SPINAL MUSCULAR ATROPHY TYPE 1
    Day, John W.
    Chiriboga, Claudia A.
    Crawford, Thomas O.
    Darras, Basil T.
    Finkel, Richard S.
    Connolly, Anne M.
    Iannaccone, Susan T.
    Kuntz, Nancy L.
    Pena, Loren D. M.
    Schultz, Meredith
    Shieh, Perry B.
    Smith, Edward C.
    Kausar, Imran
    Feltner, Douglas E.
    Ogrinc, Francis G.
    Ouyang, Haojun
    Macek, Thomas A.
    Kernbauer, Elaine
    Muehring, Lynlee M.
    L'Italien, James
    Sproule, Douglas M.
    Kaspar, Brian K.
    Mendell, Jerry R.
    JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, 2019, 90 (12): : E69 - E69
  • [4] Apitegromab in spinal muscular atrophy: baseline characteristics of participants enrolled in the phase 3 SAPPHIRE study
    Crawford, T.
    Servais, L.
    Krueger, J.
    Koelbel, H.
    Garcia, M. Gomez
    Cances, C.
    Kuntz, N.
    Finkel, R.
    Yao, B.
    Zhao, G.
    Marantz, J.
    Darras, B.
    Mercuri, E.
    NEUROMUSCULAR DISORDERS, 2024, 43
  • [5] A phase 1 trial of Riluzole in spinal muscular atrophy
    Russman, BS
    Iannaccone, ST
    Samaha, FJ
    ARCHIVES OF NEUROLOGY, 2003, 60 (11) : 1601 - 1603
  • [6] Prospective cohort study of spinal muscular atrophy types 2 and 3
    Kaufmann, Petra
    McDermott, Michael P.
    Darras, Basil T.
    Finkel, Richard S.
    Sproule, Douglas M.
    Kang, Peter B.
    Oskoui, Maryam
    Constantinescu, Andrei
    Gooch, Clifton L.
    Foley, A. Reghan
    Yang, Michele L.
    Tawil, Rabi
    Chung, Wendy K.
    Martens, William B.
    Montes, Jacqueline
    Battista, Vanessa
    O'Hagen, Jessica
    Dunaway, Sally
    Flickinger, Jean
    Quigley, Janet
    Riley, Susan
    Glanzman, Allan M.
    Benton, Maryjane
    Ryan, Patricia A.
    Punyanitya, Mark
    Montgomery, Megan J.
    Marra, Jonathan
    Koo, Benjamin
    De Vivo, Darryl C.
    NEUROLOGY, 2012, 79 (18) : 1889 - 1897
  • [7] Phase II Open Label Study of Valproic Acid in Spinal Muscular Atrophy
    Swoboda, Kathryn J.
    Scott, Charles B.
    Reyna, Sandra P.
    Prior, Thomas W.
    LaSalle, Bernard
    Sorenson, Susan L.
    Wood, Janine
    Acsadi, Gyula
    Crawford, Thomas O.
    Kissel, John T.
    Krosschell, Kristin J.
    D'Anjou, Guy
    Bromberg, Mark B.
    Schroth, Mary K.
    Chan, Gary M.
    Elsheikh, Bakri
    Simard, Louise R.
    PLOS ONE, 2009, 4 (05):
  • [8] Phase 2 Study of ISIS-SMNRx in Children with Spinal Muscular Atrophy
    Swoboda, Kathryn J.
    Chiraboga, Claudia
    Darras, Basil
    Iannacone, Susan
    Montes, Jackie
    Castro, Diana
    Holuba, Nicole
    Rausch, Nicole
    Ramos, Chris
    Visyak, Nicole
    Dunaway, Sally
    Trussell, Donata
    Pasternak, Amy
    Nielson, Leslie
    DeVivo, Darryl
    McGuire, Dawn
    Norris, Dan
    Alexander, Katie
    Bennett, C. Frank
    Bishop, Kathie
    ANNALS OF NEUROLOGY, 2014, 76 : S67 - S67
  • [9] Large deletions within the spinal muscular atrophy gene region in a patient with spinal muscular atrophy type 3
    Wei, Wei
    Chen, Chunyue
    Liu, Wenting
    Du, Zhenfang
    Chen, Xiaoling
    Zhang, Xianning
    NEURAL REGENERATION RESEARCH, 2011, 6 (23) : 1810 - 1813
  • [10] Large deletions within the spinal muscular atrophy gene region in a patient with spinal muscular atrophy type 3
    Wei Wei1
    Neural Regeneration Research, 2011, 6 (23) : 1810 - 1813
12345