RNA Base Editing for the Treatment of Alpha-1 Antitrypsin Deficiency

被引：0

作者：

Monian, Prashant ^{[1
]}

Shivalila, Chikdu ^{[1
]}

Lu, Genliang ^{[1
]}

Bowman, Keith ^{[1
]}

Bylsma, Marissa ^{[1
]}

Byrne, Michael ^{[1
]}

Cannon, Megan ^{[1
]}

Desai, Jigar ^{[1
]}

Faraone, Alyse ^{[1
]}

Favaloro, Frank ^{[1
]}

Ghosh, Anamitra ^{[1
]}

Godfrey, Jack ^{[1
]}

Hernandez, Nidia ^{[1
]}

Iwamoto, Naoki ^{[1
]}

Kawamoto, Tomomi ^{[1
]}

Kumarasamy, Jayakanthan ^{[1
]}

Kandasamy, Pachamuthu ^{[1
]}

Lamattina, Anthony ^{[1
]}

Lemaitre, Muriel ^{[1
]}

Lindsey, Amber ^{[1
]}

Liu, Fangjun ^{[1
]}

Looby, Richard ^{[1
]}

Luu, Khoa ^{[1
]}

Metterville, Jake ^{[1
]}

Paik, Ik-Hyeon ^{[1
]}

Pan, Qianli ^{[1
]}

Pu, Tom ^{[1
]}

Purcell-Estabrook, Erin ^{[1
]}

Rheinhardt, Jeanette ^{[1
]}

Shimizu, Mamoru ^{[1
]}

Singh, Kuldeep ^{[1
]}

Standley, Stephany ^{[1
]}

Omas, Carina Th ^{[1
]}

Tripathi, Snehlata ^{[1
]}

Yang, Hailin ^{[1
]}

Yordanoff, Ryan ^{[1
]}

Yin, Yuan ^{[1
]}

Yu, Hui ^{[1
]}

Narayanan, Padma ^{[1
]}

Giangrande, Paloma H. ^{[1
]}

Vargeese, Chandra ^{[1
]}

机构：

[1] Wave Life Sci, Cambridge, MA USA

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：45 / 45

页数：1

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