New frontiers to cure Alport syndrome: COL4A3 and COL4A5 gene editing in podocyte-lineage cells

被引：0
|
作者：
Daga, Sergio
Donati, Francesco
Capitani, Katia
Croci, Susanna
Tita, Rossella
Giliberti, Annarita
Valentino, Floriana
Benetti, Elisa
Fallerini, Chiara
Niccheri, Francesca
Baldassarri, Margherita
Mencarelli, Maria Antonietta
Frullanti, Elisa
Furini, Simone
Conticello, Silvestro Giovanni
Renieri, Alessandra
Pinto, Anna Maria
机构：
[1] University of Siena,Medical Genetics
[2] Core Research Laboratory,Department of Medical Biotechnologies
[3] ISPRO,Genetica Medica
[4] University of Siena,undefined
[5] Azienda Ospedaliera Universitaria Senese,undefined
来源：
EUROPEAN JOURNAL OF HUMAN GENETICS | 2024年 / 32卷 / 01期
关键词：
D O I：
10.1038/s41431-023-01287-y
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
引用
收藏
页码：131 / 131
页数：1
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