Limitations of Bu/Flu-based preparative regimen in CTLA-4 haploinsufficiency to achieving disease phenotype correction

被引:2
|
作者
Parker, Loretta [1 ]
Kapadia, Malika [2 ]
Chellapandian, Deepak [3 ]
Whangbo, Jennifer [2 ]
Grace, Rachael [4 ]
Prince, Chengyu [5 ]
Parikh, Suhag [6 ]
Bray, Robert [7 ]
Gebel, Howard [7 ]
Chandrakasan, Shanmuganathan [8 ]
机构
[1] Emory, Childrens Healthcare Atlanta, Atlanta, GA USA
[2] Boston Childrens, Pediat Hematopoiet Stem Cell Transplantat, Dana Farber, Boston, MA USA
[3] Johns Hopkins All Childrens Hosp, Blood & Marrow Transplant, St Petersburg, FL USA
[4] Boston Childrens, Dana Farber, Hematol Clin Res, Boston, MA USA
[5] Emory Univ, Atlanta, GA USA
[6] Emory, Childrens Healthcare Atlanta, Cellular Therapies Nonmalignant Dis, Atlanta, GA USA
[7] Emory Univ, Dept Pathol & Lab Med, Atlanta, GA USA
[8] Emory Univ SOM, Childrens Healthcare Atlanta, Atlanta, GA USA
关键词
CTLA-4; Busulfan; Fludarabine; HSCT; Mixed chimerism;
D O I
10.1016/j.clim.2023.109396
中图分类号
R392 [医学免疫学]; Q939.91 [免疫学];
学科分类号
100102 ;
摘要
49
引用
收藏
页码:16 / 17
页数:2
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  • [1] LIMITATIONS OF BUSULFAN/FLUDARABINE-BASED PREPARATIVE REGIMEN IN CTLA-4 HAPLOINSUFFICIENCY TO ACHIEVING DISEASE PHENOTYPE CORRECTION
    Parker, Loretta
    Kapadia, Malika
    Chellapandian, Deepak
    Whangbo, Jennifer
    Grace, Rachael
    Prince, Chengyu
    Parikh, Suhag
    Bray, Robert
    Gebel, Howard
    Chandrakasan, Shanmuganathan
    BONE MARROW TRANSPLANTATION, 2023, 58 (SUPP1) : 60 - 60