Long-term safety, tolerability, and efficacy of efgartigimod in patients with generalized myasthenia gravis: Concluding analyses from the ADAPT plus study

被引:0
|
作者
Bril, Vera [1 ,2 ]
Pasnoor, Mamatha [3 ]
Karam, Chafic [4 ]
Peric, Stojan [5 ]
De Bleecker, Jan L. [6 ]
Murai, Hiroyuki [7 ]
Meisel, Andreas [8 ]
Beydoun, Said [9 ]
Vu, Tuan [10 ]
Ulrichts, Peter [11 ]
Van Hoorick, Benjamin [11 ]
T'Joen, Caroline [11 ]
Kaprielian, Roger [11 ]
Utsugisawa, Kimiaki [12 ]
Verschuuren, Jan [13 ]
Mantegazza, Renato [14 ]
Howard, James F., Jr. [15 ]
机构
[1] Univ Hlth Network, Dept Neurol, Ellen & Martin Prosserman Ctr Neuromuscular Dis, Toronto, ON, Canada
[2] Univ Toronto, Dept Neurol, Toronto, ON, Canada
[3] Univ Kansas, Dept Neurol, Med Ctr, Kansas City, KS USA
[4] Univ Penn, Penn Neurosci Ctr, Philadelphia, PA USA
[5] Univ Belgrade, Clin Ctr Serbia, Neurol Clin, Belgrade, Serbia
[6] Ghent Univ Hosp, Dept Neurol, Ghent, Belgium
[7] Int Univ Hlth & Welf, Dept Neurol, Sch Med, Tokyo, Japan
[8] Charite Univ Med Berlin, Dept Neurol, Berlin, Germany
[9] Univ Southern Calif, Keck Sch Med, Dept Neurol, Los Angeles, CA USA
[10] Univ S Florida, Dept Neurol, Morsani Coll Med, Tampa, FL USA
[11] Argenx, Clin Dev, Ghent, Belgium
[12] Hanamaki Gen Hosp, Dept Neurol, Hanamaki, Japan
[13] Leiden Univ Med Ctr, Dept Neurol, Leiden, Netherlands
[14] Fdn IRCCS Ist Neurol Carlo Besta, Dept Neuroimmunol & Neuromuscular Dis, Milan, Italy
[15] Univ N Carolina, Dept Neurol, Chapel Hill, NC USA
关键词
D O I
10.1016/j.jns.2023.121089
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
121089
引用
收藏
页数:2
相关论文
共 50 条
  • [1] Long-Term Safety, Tolerability, And Efficacy of Efgartigimod in Patients with Generalized Myasthenia Gravis: Concluding Analyses from the ADAPT plus Study
    Pasnoor, Mamatha
    Bril, Vera
    Karam, Chafic
    Peric, Stojan
    De Bleecker, Jan
    Murai, Hiroyuki
    Meisel, Andreas
    Beydoun, Said
    Vu, Tuan
    Ulrichts, Peter
    Van Hoorick, Benjamin
    T'joen, Caroline
    Utsugisawa, Kimiaki
    Verschuuren, Jan
    Mantegazza, Renato
    Howard, James
    [J]. NEUROLOGY, 2023, 100 (17)
  • [2] Long-term safety, tolerability, and efficacy of Efgartigimod in patients with Generalized Myasthenia Gravis: concluding analyses from the ADAPT plus study
    Ashcraft, E.
    Bril, V.
    Pasnoor, M.
    Karam, C.
    Peric, S.
    De Bleecker, J.
    Murai, H.
    Meisel, A.
    Beydoun, S.
    Vu, T.
    Ulrichts, P.
    Van Hoorick, B.
    T'joen, C.
    Utsugisawa, K.
    Verschuuren, J.
    Mantegazza, R.
    Howard, J.
    [J]. NEUROMUSCULAR DISORDERS, 2023, 33 : S179 - S179
  • [3] LONG-TERM SAFETY, TOLERABILITY, AND EFFICACY OF EFGARTIGIMOD IN PATIENTS WITH GENERALIZED MYASTHENIA GRAVIS: INTERIM RESULTS OF THE ADAPT plus STUDY
    Howard, James F., Jr.
    Bril, Vera
    Tuan Vu
    Karam, Chafic
    Peric, Stojan
    De Bleecker, Jan L.
    Murai, Hiroyuki
    Meisel, Andreas
    Beydoun, Said
    Pasnoor, Mamatha
    Guglietta, Antonio
    T'joen, Caroline
    Utsugisawa, Kimiaki
    Verschuuren, Jan
    Mantegazza, Renato
    [J]. MUSCLE & NERVE, 2022, 65 : S9 - S10
  • [4] LONG-TERM SAFETY, TOLERABILITY AND EFFICACY OF EFGARTIGIMOD IN PATIENTS WITH GENERALIZED MYASTHENIA GRAVIS: INTERIM RESULTS OF THE ADAPT plus STUDY
    Howard, James
    Bril, Vera
    Tuan Vu
    Karam, Chafic
    Peric, Stojan
    De Bleecker, Jan
    Murai, Hiroyuki
    Meisel, Andreas
    Beydoun, Said
    Pasnoor, Mamatha
    Guglietta, Antonio
    T'joen, Caroline
    Utsugisawa, Kimiaki
    Mantegazza, Renato
    [J]. MUSCLE & NERVE, 2022, 66 : S57 - S57
  • [5] Long-term Safety and Efficacy of Efgartigimod in Patients With Generalized Myasthenia Gravis: Interim Results of the ADAPT plus Study
    Howard, James
    Bril, Vera
    Vu, Tuan
    Karam, Chafic
    Peric, Stojan
    De Bleecker, Jan
    Murai, Hiroyuki
    Meisel, Andreas
    Beydoun, Said
    Pasnoor, Mamatha
    Guglietta, Antonio
    Ulrichts, Peter
    T'joen, Caroline
    Brauer, Edward
    Utsugisawa, Kimiaki
    Verschuuren, Jan
    Mantegazza, Renato
    [J]. NEUROLOGY, 2022, 99 (23) : S37 - S38
  • [6] Long-Term Safety, Tolerability, And Efficacy of Efgartigimod In Patients With gMG: Final Analyses From The ADAPT plus Study
    Meisel, A.
    De Bleecker, J.
    Verschuuren, J.
    Bril, V.
    Vu, T.
    Karam, C.
    Peric, S.
    Murai, H.
    Beydoun, S.
    Pasnoor, M.
    Steeland, S.
    Van Hoorick, B.
    T'joen, C.
    Utsugisawa, K.
    Mantegazza, R.
    Howard, J.
    [J]. EUROPEAN JOURNAL OF NEUROLOGY, 2023, 30 : 208 - 209
  • [7] Long-Term Safety, Tolerability, and Efficacy of Subcutaneous Efgartigimod PH20 in Patients with Generalized Myasthenia Gravis: Interim Results of the ADAPT-SC plus Study
    Howard, James
    Li, George
    Vu, Tuan
    Korobko, Denis
    Smilowski, Marek
    Liu, Li
    Steeland, Sophie
    Noukens, Jan
    Van Hoorick, Benjamin
    Podhorna, Jana
    Li, Yuebing
    Utsugisawa, Kimiaki
    Sacca, Francesco
    Wiendl, Heinz
    De Bleecker, Jan
    Mantegazza, Renato
    [J]. NEUROLOGY, 2023, 100 (17)
  • [8] Efficacy, Safety, and Tolerability of Efgartigimod in Patients With Generalized Myasthenia Gravis: Analysis of the Phase 3 ADAPT Study
    Howard, James
    Bril, Vera
    Vu, Tuan
    Karam, Chafic
    Peric, Stojan
    Murai, Hiroyuki
    Guglietta, Antonio
    Ulrichts, Peter
    Vangeneugden, Tony
    Utsugisawa, Kimiaki
    Verschuuren, Jan
    Mantegazza, Renato
    [J]. NEUROLOGY, 2021, 96 (15)
  • [9] Long-Term Safety, Tolerability, and Efficacy of Subcutaneous Efgartigimod PH20 in Patients with Generalized Myasthenia Gravis: Interim Results of the ADAPT-SC plus Study
    Ritt, Elissa
    Howard, James F., Jr.
    Li, George
    Vu, Tuan
    Korobko, Denis
    Smilowski, Marek
    Liu, Li
    Steeland, Sophie
    Noukens, Jan
    Van Hoorick, Benjamin
    Podhorna, Jana
    Li, Yuebing
    Utsugisawa, Kimiaki
    Sacca, Francesco
    Wiendl, Heinz
    De Bleecker, Jan L.
    Mantegazza, Renato
    [J]. ANNALS OF NEUROLOGY, 2023, 94 : S244 - S245
  • [10] Long-term safety, tolerability, and efficacy of efgartigimod (ADAPT plus ): interim results from a phase 3 open-label extension study in participants with generalized myasthenia gravis
    Howard Jr, James F.
    Bril, Vera
    Vu, Tuan
    Karam, Chafic
    Peric, Stojan
    De Bleecker, Jan L.
    Murai, Hiroyuki
    Meisel, Andreas
    Beydoun, Said R.
    Pasnoor, Mamatha
    Guglietta, Antonio
    Van Hoorick, Benjamin
    Steeland, Sophie
    T'joen, Caroline
    Utsugisawa, Kimiaki
    Verschuuren, Jan
    Mantegazza, Renato
    [J]. FRONTIERS IN NEUROLOGY, 2024, 14