Developing an iPSC-based neural gene therapy approach for MPS IIIA

被引：0

作者：

Mandolfo, Oriana ^{[1
]}

Learmonth, Yuko Ishikawa ^{[1
]}

Usman, Asma'u ^{[2
]}

Andreou, Tereza ^{[1
]}

Taylor, Jessica ^{[3
]}

Parker, Helen ^{[1
]}

McKay, Tristan ^{[4
]}

Bigger, Brian ^{[1
]}

机构：

[1] Univ Manchester, Manchester, Lancs, England

[2] NGO Consulting, Abuja, Nigeria

[3] Univ Cambridge, CRUK Inst, Cambridge, England

[4] Manchester Metropolitan Univ, Manchester, Lancs, England

来源：

MOLECULAR GENETICS AND METABOLISM | 2023年 / 138卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2022.107220

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

237

引用

页码：86 / 87

页数：2

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