Pharmacological and molecular features of DT-168, a topical GeneTAC™ small molecule being developed as potential treatment for Fuchs Endothelial Corneal Dystrophy caused by CTG repeat expansions in the TCF4 gene

被引：0
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作者：
Powers, Andrew [1 ]
Cheung, Katie [1 ]
Osgood, Nicola [1 ]
Kudwa, Andrea [1 ]
Shepard, Peter [1 ]
Datta, Sumon [1 ]
Safadi, Muhammad [1 ]
Sinha, Santosh [1 ]
Kerr, Jim [1 ]
Zhang, Chengzhi [1 ]
Levin, Nancy [1 ]
Chilcoat, Doane [1 ]
Jeffries, Sean [1 ]
Kim, Jae [1 ]
Siffert, Joao [1 ]
机构：
[1] Design Therapeut, Carlsbad, CA USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2023年 / 64卷 / 08期
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R77 [眼科学];
学科分类号：
100212 ;
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页数：4
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