Increased Striatum Transduction with an Engineered AAV Capsid and Selective Transduction of Striatal Cholinergic Neurons Using a Truncated Human Choline Acetyltransferase Promoter

被引：0
|
作者：
Santoscoy, Miguel C. [1 ,2 ,3 ]
Espinoza, Paula [1 ,2 ,3 ]
De La Cruz, Demitri [1 ,2 ,3 ]
Mahamdeh, Mohammed [1 ,4 ]
Starr, Jacqueline R. [1 ,5 ]
Patel, Nikita [1 ,2 ,3 ]
Maguire, Casey A. [1 ,2 ,3 ]
机构：
[1] Harvard Med Sch, Boston, MA 02115 USA
[2] Massachusetts Gen Hosp, Dept Neurol, Boston, MA 02114 USA
[3] Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02114 USA
[4] Massachusetts Gen Hosp, Cardiovasc Res Ctr, Charlestown, MA 02114 USA
[5] Brigham & Womens Hosp, Channing Div Network Med, 75 Francis St, Boston, MA 02115 USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
938
引用
收藏
页码：455 / 456
页数：2
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