Comparison of Cardiac Specific Promoters to Liver-Specific miRNA Targets to Maximize Cardiac vs Liver Expression Following Intravenous AAVrh.10-Mediated Cardiac Gene Therapy

被引:0
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作者
Bose, Abhishek [1 ]
Hackett, Neil R. [1 ]
Khan-Yusufzai, Nadir [1 ]
Stiles, Katie M. [1 ]
Crystal, Ronald G. [1 ]
机构
[1] Weill Cornell Med, Dept Med Genet, New York, NY USA
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1518
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页码:715 / 715
页数:1
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