SYMPTOMS, TREATMENT EFFECTIVENESS AND QUALITY OF LIFE FOR PATIENTS LIVING WITH LONG-CHAIN FATTY ACID OXIDATION DISORDERS (LC-FAOD) IN THE UNITED STATES: PATIENT AND CAREGIVER REPORTED OUTCOMES FROM LC-FAOD ODYSSEY

被引:0
|
作者
Yang, E. [1 ]
Kruger, E. [1 ]
Thompson, A. [1 ]
Reineking, B. [1 ]
机构
[1] Ultragenyx Pharmaceut Inc, Novato, CA USA
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F [经济];
学科分类号
02 ;
摘要
PCR226
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页码:S354 / S355
页数:2
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