Therapeutic Gene Editing of CFTR to Treat Cystic Fibrosis, Using Nanoparticle Formulations for the Delivery of CRISPR/Cas9

被引：0
|
作者：
Greenwood, Miriam L. [1 ]
Hart, Stephen L. [2 ]
机构：
[1] UCL Inst Child Hlth, Genet & Genom Med, London, England
[2] UCL Great Ormond St Inst Child Hlth, London, England
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
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D O I：
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中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1122
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页码：537 / 537
页数：1
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