共 50 条
- [1] Emicizumab Prophylaxis for the Treatment of Infants with Severe Hemophilia A without Factor VIII Inhibitors: Results from the Interim Analysis of the HAVEN 7 StudyBLOOD, 2022, 140Pipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI 48109 USA Univ Michigan, Ann Arbor, MI 48109 USACollins, Peter论文数: 0 引用数: 0 h-index: 0机构: Cardiff Univ, Sch Med, Cardiff, Wales Univ Michigan, Ann Arbor, MI 48109 USADhalluin, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAKenet, Gili论文数: 0 引用数: 0 h-index: 0机构: Sheba Med Ctr, Ramat Gan, Israel Tel Aviv Univ, Tel Aviv, Israel Univ Michigan, Ann Arbor, MI 48109 USASchmitt, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USABuri, Muriel论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAJimenez-Yuste, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Madrid, La Paz Univ Hosp, Madrid, Spain Univ Michigan, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Young, Guy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA 90027 USA Univ Michigan, Ann Arbor, MI 48109 USAOldenburg, Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Bonn, Bonn, Germany Univ Michigan, Ann Arbor, MI 48109 USAMancuso, Maria Elisa论文数: 0 引用数: 0 h-index: 0机构: IRCCS Humanitas Res Hosp, Rozzano, Italy Univ Michigan, Ann Arbor, MI 48109 USAKiialainen, Anna论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAChang, Tiffany论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, San Francisco, CA USA Univ Michigan, Ann Arbor, MI 48109 USALehle, Michaela论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAFijnvandraat, Karin论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam, Netherlands Univ Michigan, Ann Arbor, MI 48109 USA
- [2] FVIII Exposure Analysis from the HAVEN 7 Study of Emicizumab in Infants with Severe Hemophilia ABLOOD, 2024, 144 : 2589 - 2590Young, Guy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA USA Childrens Hosp Los Angeles, Los Angeles, CA USAEakle, Katherine论文数: 0 引用数: 0 h-index: 0机构: Genentech Inc, South San Francisco, CA USA Childrens Hosp Los Angeles, Los Angeles, CA USALim, Elise论文数: 0 引用数: 0 h-index: 0机构: Genentech Inc, South San Francisco, CA USA Childrens Hosp Los Angeles, Los Angeles, CA USAWang, Michael论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Anschutz Med Campus, Aurora, CO USA Childrens Hosp Los Angeles, Los Angeles, CA USA
- [3] EMICIZUMAB PROPHYLAXIS FOR THE TREATMENT OF INFANTS WITH SEVERE HEMOPHILIA A WITHOUT FACTOR VIII INHIBITORS: PRIMARY ANALYSIS OF THE HAVEN 7 STUDYAMERICAN JOURNAL OF HEMATOLOGY, 2024, 100 : 99 - 99Pipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI 48109 USA Univ Michigan, Ann Arbor, MI 48109 USACollins, Peter论文数: 0 引用数: 0 h-index: 0机构: Cardiff Univ, Sch Med, Cardiff, Wales Univ Michigan, Ann Arbor, MI 48109 USADhalluin, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAKenet, Gili论文数: 0 引用数: 0 h-index: 0机构: Sheba Med Ctr, Ramat Gan, Israel Tel Aviv Univ, Tel Aviv, Israel Univ Michigan, Ann Arbor, MI 48109 USASchmitt, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USABuri, Muriel论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAJimenez-Yuste, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Madrid, Hosp Univ La Paz IdiPaZ, Madrid, Spain Univ Michigan, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Young, Guy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA 90027 USA Univ Michigan, Ann Arbor, MI 48109 USAOldenburg, Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Bonn, Univ Hosp Bonn, Fac Med, Inst Expt Hematol & Transfus Med, Bonn, Germany Univ Michigan, Ann Arbor, MI 48109 USAMancuso, Maria Elisa论文数: 0 引用数: 0 h-index: 0机构: IRCCS Humanitas Res Hosp, Rozzano, Italy Humanitas Univ, Milan, Italy Univ Michigan, Ann Arbor, MI 48109 USAKavakli, Kaan论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Fac Med, Childrens Hosp, Izmir, Turkiye Univ Michigan, Ann Arbor, MI 48109 USAKiialainen, Anna论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USANiggli, Markus论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAChang, Tiffany论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, San Francisco, CA USA Univ Michigan, Ann Arbor, MI 48109 USALehle, Michaela论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAFijnvandraat, Karin论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam, Netherlands Univ Michigan, Ann Arbor, MI 48109 USA
- [4] Pharmacodynamic Biomarkers in Infants with Hemophilia A Receiving Emicizumab in HAVEN 7BLOOD, 2023, 142Kiialainen, Anna论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland F Hoffmann La Roche Ltd, Basel, SwitzerlandPipe, Steven论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI USA F Hoffmann La Roche Ltd, Basel, SwitzerlandFijnvandraat, Karin论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam, Netherlands F Hoffmann La Roche Ltd, Basel, SwitzerlandKenet, Gili论文数: 0 引用数: 0 h-index: 0机构: Sheba Med Ctr, Ramat Gan, Israel Tel Aviv Univ, Tel Aviv, Israel F Hoffmann La Roche Ltd, Basel, SwitzerlandSchmitt, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland F Hoffmann La Roche Ltd, Basel, SwitzerlandBuri, Muriel论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland F Hoffmann La Roche Ltd, Basel, SwitzerlandJimenez-Yuste, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Madrid, La Paz Univ Hosp Idi Paz, Madrid, Spain F Hoffmann La Roche Ltd, Basel, SwitzerlandOldenburg, Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Bonn, Bonn, Germany F Hoffmann La Roche Ltd, Basel, SwitzerlandMancuso, Maria Elisa论文数: 0 引用数: 0 h-index: 0机构: IRCCS Humanitas Res Hosp, Ctr Thrombosis & Haemorrhag Dis, Milan, Italy F Hoffmann La Roche Ltd, Basel, SwitzerlandDhalluin, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland F Hoffmann La Roche Ltd, Basel, SwitzerlandLehle, Michaela论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland F Hoffmann La Roche Ltd, Basel, SwitzerlandCollins, Peter论文数: 0 引用数: 0 h-index: 0机构: Cardiff Univ, Sch Med, Cardiff, Wales F Hoffmann La Roche Ltd, Basel, Switzerland
- [5] Emicizumab Prophylaxis in Infants with Severe Hemophilia A without Factor VIII Inhibitors: Results from the Primary Analysis of the HAVEN 7 StudyBLOOD, 2023, 142Pipe, Steven论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI 48109 USA Univ Michigan, Ann Arbor, MI 48109 USACollins, Peter论文数: 0 引用数: 0 h-index: 0机构: Cardiff Univ, Sch Med, Cardiff, Wales Univ Michigan, Ann Arbor, MI 48109 USADhalluin, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAKenet, Gili论文数: 0 引用数: 0 h-index: 0机构: Sheba Med Ctr, Ramat Gan, Israel Tel Aviv Univ, Tel Aviv, Israel Univ Michigan, Ann Arbor, MI 48109 USASchmitt, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USABuri, Muriel论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAJimenez-Yuste, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Madrid, La Paz Univ Hosp Idi Paz, Madrid, Spain Univ Michigan, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Young, Guy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA 90027 USA Univ Michigan, Ann Arbor, MI 48109 USAOldenburg, Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Bonn, Bonn, Germany Univ Michigan, Ann Arbor, MI 48109 USAMancuso, Maria Elisa论文数: 0 引用数: 0 h-index: 0机构: IRCCS Humanitas Res Hosp, Rozzano, Italy Humanitas Univ, Rozzano, Italy Univ Michigan, Ann Arbor, MI 48109 USAKavakli, Kaan论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Fac Med, Childrens Hosp, Izmir, Turkiye Univ Michigan, Ann Arbor, MI 48109 USAKiialainen, Anna论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAChang, Tiffany论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, San Francisco, CA USA Univ Michigan, Ann Arbor, MI 48109 USALehle, Michaela论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USANiggli, Markus论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAFijnvandraat, Karin论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam, Netherlands Univ Michigan, Ann Arbor, MI 48109 USA
- [6] Emicizumab prophylaxis for the treatment of infants with severe haemophilia A without factor VIII inhibitors: primary analysis of the HAVEN 7 studyHAEMOPHILIA, 2024, 30 : 24 - 25Pipe, S. W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI 48109 USA Univ Michigan, Ann Arbor, MI 48109 USACollins, P.论文数: 0 引用数: 0 h-index: 0机构: Cardiff Univ, Sch Med, Cardiff, Wales Univ Michigan, Ann Arbor, MI 48109 USADhalluin, C.论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAKenet, G.论文数: 0 引用数: 0 h-index: 0机构: Sheba Med Ctr, Ramat Gan, Israel Tel Aviv Univ, Tel Aviv, Israel Univ Michigan, Ann Arbor, MI 48109 USASchmitt, C.论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USABuri, M.论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAJimenez-Yuste, V.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma, Hosp Univ Paz IdiPaz, Madrid, Spain Univ Michigan, Ann Arbor, MI 48109 USA论文数: 引用数: h-index:机构:Young, G.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA USA Univ Michigan, Ann Arbor, MI 48109 USAOldenburg, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Bonn, Univ Hosp Bonn, Med Fac, Inst Expt Hematol & Transfus Med, Bonn, Germany Univ Michigan, Ann Arbor, MI 48109 USAMancuso, M. E.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Humanitas Res Hosp, Rozzano, Italy Humanitas Univ, Milan, Italy Univ Michigan, Ann Arbor, MI 48109 USAKavakli, K.论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Fac Med, Childrens Hosp, Izmir, Turkiye Univ Michigan, Ann Arbor, MI 48109 USAKiialainen, A.论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USANiggli, M.论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAChang, T.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, San Francisco, CA USA Univ Michigan, Ann Arbor, MI 48109 USALehle, M.论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI 48109 USAFijnvandraat, K.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam, Netherlands Univ Michigan, Ann Arbor, MI 48109 USA
- [7] Emicizumab prophylaxis in infants with hemophilia A (HAVEN 7): primary analysis of a phase 3b open-label trialBLOOD, 2024, 143 (14) : 1355 - 1364Pipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Ann Arbor, MI USA Univ Michigan, Dept Pediat & Pathol, 1500 E Med Ctr Dr,MPB D4207, Ann Arbor, MI 48109 USA Univ Michigan, Ann Arbor, MI USACollins, Peter论文数: 0 引用数: 0 h-index: 0机构: Cardiff Univ, Sch Med, Cardiff, Wales Univ Michigan, Ann Arbor, MI USADhalluin, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI USAKenet, Gili论文数: 0 引用数: 0 h-index: 0机构: Sheba Med Ctr, Ramat Gan, Israel Tel Aviv Univ, Tel Aviv, Israel Univ Michigan, Ann Arbor, MI USASchmitt, Christophe论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI USABuri, Muriel论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI USAJimenez-Yuste, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Madrid, La Paz Univ Hosp IdiPaz, IdiPaz, Madrid, Spain Univ Michigan, Ann Arbor, MI USA论文数: 引用数: h-index:机构:Young, Guy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA USA Univ Michigan, Ann Arbor, MI USAOldenburg, Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Bonn, Univ Hosp Bonn, Inst Expt Hematol & Transfus Med, Med Fac, Bonn, Germany Univ Michigan, Ann Arbor, MI USAMancuso, Maria Elisa论文数: 0 引用数: 0 h-index: 0机构: IRCCS Humanitas Res Hosp, Milan, Italy Humanitas Univ, Milan, Italy Univ Michigan, Ann Arbor, MI USAKavakli, Kaan论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Ege Univ, Childrens Hosp, Dept Hematol, Bornova, Izmir, Turkiye Univ Michigan, Ann Arbor, MI USAKiialainen, Anna论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI USADeb, Sonia论文数: 0 引用数: 0 h-index: 0机构: Genentech Inc, South San Francisco, CA USA Univ Michigan, Ann Arbor, MI USANiggli, Markus论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI USAChang, Tiffany论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut Inc, San Francisco, CA USA Univ Michigan, Ann Arbor, MI USALehle, Michaela论文数: 0 引用数: 0 h-index: 0机构: F Hoffmann La Roche Ltd, Basel, Switzerland Univ Michigan, Ann Arbor, MI USAFijnvandraat, Karin论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam, Netherlands Univ Michigan, Ann Arbor, MI USA
- [8] HAVEN 7, Primary Analysis: Infants benefit from early Prophylaxis with EmicizumabTRANSFUSION MEDICINE AND HEMOTHERAPY, 2024, 51 (03) : 201 - 201不详论文数: 0 引用数: 0 h-index: 0
- [9] EMICIZUMAB PROPHYLAXIS IN INFANTS WITH SEVERE HEMOPHILIA A: MANAGEMENT OF 6 CASESPEDIATRIC BLOOD & CANCER, 2022, 69Wang, Cassandra论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Ctr Thrombosis & Hemostasis, Los Angeles, CA USA Childrens Hosp Los Angeles, Ctr Thrombosis & Hemostasis, Los Angeles, CA USAKizilocak, Hande论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Ctr Thrombosis & Hemostasis, Los Angeles, CA USA Childrens Hosp Los Angeles, Ctr Thrombosis & Hemostasis, Los Angeles, CA USAYoung, Guy论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Ctr Thrombosis & Hemostasis, Los Angeles, CA USA Childrens Hosp Los Angeles, Ctr Thrombosis & Hemostasis, Los Angeles, CA USA
- [10] Emicizumab in Children with Severe Hemophilia AINDIAN JOURNAL OF PEDIATRICS, 2024,Thota, Usha Rani论文数: 0 引用数: 0 h-index: 0机构: Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, India Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, IndiaMartha, Sreelatha论文数: 0 引用数: 0 h-index: 0机构: Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, India Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, IndiaRavula, Chaitanya Jyothi论文数: 0 引用数: 0 h-index: 0机构: Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, India Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, IndiaCherukuri, Nirmala论文数: 0 引用数: 0 h-index: 0机构: Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, India Niloufer Hosp Women & Children, Inst Child Hlth, Osmania Med Coll, Dept Pediat, Hyderabad, Telangana, India