Engineered Virus-Like Particle to Deliver CRISPR-Cas9 Ribonucleoprotein with Minimal Off-Target Effects

被引:0
|
作者
Jiang, Zihua [1 ]
Ai, Limei [1 ,2 ]
Yu, Miao [1 ]
Wang, Bang [3 ]
Zheng, Zongli [1 ,2 ]
机构
[1] Karolinska Inst, Ming Wai Lau Ctr Reparat Med, Hong Kong, Peoples R China
[2] City Univ Hong Kong, Dept Biomed Sci, Hong Kong, Peoples R China
[3] GenEditBio Ltd, Hong Kong, Peoples R China
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1467
引用
收藏
页码:692 / 692
页数:1
相关论文
共 50 条
  • [1] Engineered Virus-Like Particle to Deliver CRISPR-Cas9 Ribonucleoprotein In Vivo with Saturated Efficacy and Minimal Off-Target Effects
    Jiang, Zihua
    Lu, Hua
    Chan, Martin
    Wang, Bang
    Zheng, Zongli
    MOLECULAR THERAPY, 2024, 32 (04) : 374 - 374
  • [2] Efficient genome modification by CRISPR-Cas9 nickase with minimal off-target effects
    Shen B.
    Zhang W.
    Zhang J.
    Zhou J.
    Wang J.
    Chen L.
    Wang L.
    Hodgkins A.
    Iyer V.
    Huang X.
    Skarnes W.C.
    Nature Methods, 2014, 11 (4) : 399 - 402
  • [3] Structure and dynamics of off-target effects in CRISPR-Cas9
    Arantes, Pablo R.
    Mitchell, Brandon P.
    Saha, Aakash
    Nierzwicki, Lukasz
    Pacesa, Martin
    Jinek, Martin
    Palermo, Giulia
    BIOPHYSICAL JOURNAL, 2023, 122 (03) : 190A - 190A
  • [4] Molecular mechanism of off-target effects in CRISPR-Cas9
    Palermo, Giulia
    Ricci, Clarisse Gravina
    Chen, Janice
    Miao, Yinglong
    Jinek, Martin
    Doudna, Jennifer
    McCammon, J. Andrew
    ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 2019, 258
  • [5] Molecular Mechanism of Off-Target Effects in CRISPR-Cas9
    Palermo, Giulia
    Ricci, Clarisse Gravina
    Chen, Janice S.
    Miao, Yinglong
    Jinek, Martin
    Doudna, Jennifer A.
    McCammon, James A.
    BIOPHYSICAL JOURNAL, 2019, 116 (03) : 319A - 319A
  • [6] Molecular basis of off-target effects in CRISPR-Cas9
    Palermo, Giulia
    Ricci, Clarisse Gravina
    Chen, Janice
    Miao, Yinglong
    Jinek, Martin
    Doudna, Jennifer
    McCammon, James
    ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 2019, 257
  • [7] Efficient genome modification by CRISPR-Cas9 nickase with minimal off-target effects
    Shen, Bin
    Zhang, Wensheng
    Zhang, Jun
    Zhou, Jiankui
    Wang, Jianying
    Chen, Li
    Wang, Lu
    Hodgkins, Alex
    Iyer, Vivek
    Huang, Xingxu
    Skarnes, William C.
    NATURE METHODS, 2014, 11 (04) : 399 - +
  • [8] Minimizing off-target effects in CRISPR-Cas9 genome editing
    Shi-Jie Chen
    Cell Biology and Toxicology, 2019, 35 : 399 - 401
  • [9] Minimizing off-target effects in CRISPR-Cas9 genome editing
    Chen, Shi-Jie
    CELL BIOLOGY AND TOXICOLOGY, 2019, 35 (05) : 399 - 401
  • [10] Battling CRISPR-Cas9 off-target genome editing
    Daisy Li
    Hong Zhou
    Xiao Zeng
    Cell Biology and Toxicology, 2019, 35 : 403 - 406