Efficacy and Safety of Luspatercept in Patients Enrolled in the BELIEVE Trial: Data from the Phase 3b Long-Term Rollover Study

被引：2
|
作者：
Cappellini, Maria Domenica [1 ]
Taher, Ali T. [2 ]
Viprakasit, Vip [3 ]
Georgiev, Pencho [4 ]
Kuo, Kevin H. M. [5 ,6 ]
Holot, Natalia [7 ]
Vilmont, Valerie [8 ]
Medlin, Loyse Felber [8 ]
Kuo, Wen-Ling [7 ]
Lai, Yinzhi [7 ]
Bueno, Luciana Moro [8 ]
Sheth, Sujit [9 ]
机构：
[1] Univ Milan, Fdn IRCCS Ca Granda Policlin Hosp, Milan, Italy
[2] Amer Univ, Dept Internal Med, Beirut Med Ctr, Beirut, Lebanon
[3] Mahidol Univ, Siriraj Res Hosp, Bangkok, Thailand
[4] Med Univ Plovdiv, Plovdiv, Bulgaria
[5] Univ Hlth Network, Div Med Oncol & Hematol, Dept Med, Toronto, ON, Canada
[6] Univ Toronto, Div Hematol, Dept Med, Toronto, ON, Canada
[7] Bristol Myers Squibb, Princeton, NJ USA
[8] Bristol Myers Squibb Co, Celgene Int Sarl, Boudry, Switzerland
[9] Weill Cornell Med, Div Pediat Hematol Oncol, New York, NY USA
来源：
BLOOD | 2023年 / 142卷
关键词：
D O I：
10.1182/blood-2023-174089
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：4
相关论文
共 50 条
  • [1] Long-term efficacy and safety of luspatercept for the treatment of anaemia in patients with transfusion-dependent β-thalassaemia (BELIEVE): final results from a phase 3 randomised trial
    Cappellini, Maria Domenica
    Viprakasit, Vip
    Georgiev, Pencho
    Coates, Thomas
    Origa, Raffaella
    Khelif, Abderrahim
    Liew, Hong-Keng
    Tantiworawit, Adisak
    Chew, Lee-Ping
    Khalil, Abdalla
    Ho, P. Joy
    Kuo, Kevin H. M.
    Holot, Natalia
    Perin, Martina
    Giuseppi, Ana Carolina
    Kuo, Wen-Ling
    Lai, Yinzhi
    Medlin, Loyse Felber
    Bueno, Luciana Moro
    Kattamis, Antonis
    Taher, Ali
    LANCET HAEMATOLOGY, 2025, 12 (03): : e180 - e189
  • [2] Long-term efficacy and safety of 1% glycopyrronium bromide cream in patients with severe primary axillary hyperhidrosis: Results from a Phase 3b trial
    Szeimies, Rolf-Markus
    Abels, Christoph
    Kilic, Ana
    Reich, Hubert
    Berger, Birgit
    zur Wiesche, Erik Schulze
    Schramm, Katharina
    Litzka, Leonie
    Heimstaedt-Muskett, Susanne
    Masur, Clarissa
    JOURNAL OF THE EUROPEAN ACADEMY OF DERMATOLOGY AND VENEREOLOGY, 2023, 37 (04) : 823 - 830
  • [3] Long-term safety and efficacy of rVIII-SingleChain in patients with severe haemophilia A: Interim results from a phase 3B extension study
    Mahlangu, J.
    Karim, F. Abdul
    Stasyshyn, O.
    Korczowski, B.
    Brainsky, A.
    Lucas, S.
    Li, Y.
    Pabinger, I.
    HAEMOPHILIA, 2019, 25 : 148 - 149
  • [4] Long-Term Safety and Efficacy of Subcutaneously Administered Tocilizumab for Adult Rheumatoid Arthritis: A Multicenter Phase 3b Long-term Extension Study
    Kivitz A.
    Wallace T.
    Olech E.
    Borofsky M.
    Devenport J.
    Pei J.
    Michalska M.
    Rheumatology and Therapy, 2016, 3 (2) : 291 - 304
  • [5] Efficacy and Safety of Luspatercept in Patients with HbE/β-Thalassemia from the BELIEVE Study: A Subgroup Analysis
    Kuo, Kevin H. M.
    Sutcharitchan, Pranee
    Bee, Ping Chong
    Chew, Lee Ping
    Lim, Soo Min
    Goh, Ai Sim
    Vodala, Sadanand
    Kuo, Wen-Ling
    Lai, Yinzhi
    Medlin, Loyse Felber
    Perin, Martina
    Bueno, Luciana Moro
    Coates, Thomas D.
    Viprakasit, Vip
    BLOOD, 2023, 142
  • [6] Update to the long-term safety and efficacy of iptacopan in C3G: 33-month extension study data from patients enrolled in a phase 2 study
    Nester, Carla M.
    Eisenberger, Ute
    Karras, Alexandre
    Le Quintrec, Moglie
    Lightstone, Liz
    Praga, Manuel
    Remuzzi, Giuseppe
    Romeo, Maria Jose Soler
    Liu, Junhao
    Meier, Matthias
    Webb, Nicholas
    Wong, Edwin
    NEPHROLOGY DIALYSIS TRANSPLANTATION, 2024, 39
  • [7] Update to the long-term safety and efficacy of iptacopan in C3G: 33-month extension study data from patients enrolled in a phase 2 study
    Nester, Carla M.
    Eisenberger, Ute
    Karras, Alexandre
    Le Quintrec, Moglie
    Lightstone, Liz
    Praga, Manuel
    Remuzzi, Giuseppe
    Soler Romeo, Maria Jose
    Liu, Junhao
    Meier, Matthias
    Webb, Nicholas
    Wong, Edwin
    NEPHROLOGY DIALYSIS TRANSPLANTATION, 2024, 39 : I254 - I254
  • [8] Long-term safety, compliance, and effectiveness of ofatumumab in patients with relapsing multiple sclerosis: alithios phase 3b study
    Fox, E. J.
    Mayer, L.
    Aungst, A.
    Mancione, L.
    Rennie, N.
    Roustan, A.
    Stoneman, D.
    Su, W.
    Das Gupta, A.
    Zalesak, M.
    Ziehn, M. O.
    Robertson, D.
    Cohen, J.
    MULTIPLE SCLEROSIS JOURNAL, 2020, 26 (3_SUPPL) : 223 - 224
  • [9] Luspatercept in patients with low-risk myelodysplastic syndromes (LR-MDS) with ring sideroblasts (RS): long-term efficacy and safety data from the phase 3 MEDALIST study
    Platzbecker, U.
    Santini, V
    Komrokji, R. S.
    Zeidan, A.
    Garcia-Manero, G.
    Buckstein, R.
    Miteva, D.
    Keeperman, K.
    Holot, N.
    Zhang, J.
    Nadal, J. A.
    Rosettani, B.
    Yucel, A.
    Fenaux, P.
    ONCOLOGY RESEARCH AND TREATMENT, 2022, 45 (SUPPL 2) : 134 - 134
  • [10] Health-related quality of life in patients with β-thalassemia: Data from the phase 3 BELIEVE trial of luspatercept
    Cappellini, Maria Domenica
    Taher, Ali T.
    Piga, Antonio
    Shah, Farrukh
    Voskaridou, Ersi
    Viprakasit, Vip
    Porter, John B.
    Hermine, Olivier
    Neufeld, Ellis J.
    Thompson, Alexis A.
    Tang, Derek
    Yucel, Aylin
    Lord-Bessen, Jennifer
    Yu, Peiwen
    Guo, Shien
    Shetty, Jeevan K.
    Miteva, Dimana
    Zinger, Tatiana
    Backstrom, Jay T.
    Oliva, Esther Natalie
    EUROPEAN JOURNAL OF HAEMATOLOGY, 2023, 111 (01) : 113 - 124
12345