High efficiency in genome editing of pathogenic variants causing Inherited Retinal Dystrophies: the importance of CRISPR/TALEN guides and repair templates designs

被引：0
|
作者：
Siles, Laura [1 ]
Ruiz-Nogales, Sheila [1 ]
Navines-Ferrer, Arnau [1 ]
Pardo, Paula Gaudo [1 ]
Pomares, Esther [1 ]
机构：
[1] Inst Microcirugia Ocular, Barcelona, Catalunya, Spain
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2023年 / 64卷 / 08期
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中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
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页数：2
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