Clinical outcomes in patients switching from agalsidase beta to migalastat: A Fabry Registry analysis

被引：0
|
作者：
Pisani, Antonio [1 ]
Wilson, Kathryn [2 ]
Batista, Julie [3 ]
Kantola, Ilkka [4 ]
Arduan, Alberto Ortiz [5 ]
Politei, Juan [6 ]
Al-Shaar, Laila [3 ]
Maski, Manish [3 ]
Crespo, Ana [3 ]
Ponce, Elvira [3 ]
Linhart, Ales [7 ]
机构：
[1] Univ Federico II, Naples, Italy
[2] Navitas Data Sci, Pottstown, PA USA
[3] Sanofi, Cambridge, MA USA
[4] Turku Univ Hosp, Turku, Finland
[5] Hosp Univ Fdn Jimenez Diaz, Madrid, Spain
[6] Fdn Study Neurometabol Dis, Buenos Aires, DF, Argentina
[7] Charles Univ Prague, Prague, Czech Republic
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107999
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
260
引用
收藏
页数：1
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