Preclinical Safety Assessment of an Investigational Gene Replacement Therapy for the Treatment of RPE65-Mediated Inherited Retinal Dystrophies

被引：0
|
作者：
Wu, Weiwei [1 ]
He, Sheng [1 ]
Yang, Qi [1 ]
Yang, Chenhua [1 ]
Zhang, Jingyu [1 ]
Song, Jipeng [1 ]
Zhu, Mengke [1 ]
Shi, Linyu [1 ]
Yao, Xuan [1 ]
Yang, Hui [1 ,2 ]
机构：
[1] HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China
[2] Chinese Acad Sci, Ctr Excellence Brain Sci & Intelligence Technol, Shanghai, Peoples R China
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
313
引用
收藏
页码：171 / 171
页数：1
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