Characteristics of patients who have switched from alglucosidase alfa to avalglucosidase alfa: Baseline data from the Pompe Registry

被引：0
|
作者：
Schoser, Benedikt [1 ]
Abbott, Mary-Alice [2 ]
Toscano, Antonio [3 ]
Foster, Meredith C. [4 ]
Periquet, Magali [5 ]
Kishnani, Priya [6 ]
机构：
[1] LMU Klinikum Munchen, Dept Neurol, Friedrich Baur Inst, Munich, Germany
[2] Baystate Med Ctr, Springfield, MA USA
[3] Univ Messina, Reference Ctr Rare Neuromuscular Disorders, Dept Clin & Expt Med, Messina, Italy
[4] Sanofi, Cambridge, MA USA
[5] Sanofi, Berlin, Germany
[6] Duke Univ, Med Ctr, Durham, NC USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2023年 / 138卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2022.107310
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
327
引用
收藏
页码：118 / 118
页数：1
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