A QUANTITATIVE SYSTEMS PHARMACOLOGY (QSP) MODEL FOR CLASSICAL HOMOCYSTINURIA PREDICTING EFFICACY OF TREATMENT

被引:0
|
作者
Majtan, Tomas [1 ]
Mines, Robert [2 ]
Khalifa, Maryam [2 ]
Van der Graaf, Piet H. [2 ]
Chung, Douglas [2 ]
Chen, Ying [3 ]
Rodems, Steve [3 ]
Liu, Kai [3 ]
机构
[1] Univ Fribourg, Fac Sci & Med, Dept Pharmacol, Fribourg, Switzerland
[2] Certara QSP, Raleigh, NC USA
[3] Travere Therapeut, San Diego, CA USA
关键词
D O I
10.1016/j.ymgme.2023.107453
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
079
引用
收藏
页码:70 / 71
页数:2
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