Comparable Outcome after Busulfan- or Treosulfan-Based Conditioning Regimen in Children Above 4 Years of Age with ALL Undergoing Allogeneic HSCT. Results from the Prospective International Forum-Trial

被引:0
|
作者
Kalwak, Krzysztof [1 ]
Bader, Peter [2 ]
Dalle, Jean-Hugues [3 ]
Sedlacek, Petr [4 ]
Buechner, Jochen [5 ]
Ifversen, Marianne [6 ]
Svec, Peter [7 ]
Stein, Jerry [8 ]
Gungor, Tayfun [9 ]
Toporski, Jacek [10 ]
Diaz De Heredia, Cristina [11 ]
Bierings, Marc
Meisel, Roland [12 ]
Ansari, Marc [13 ]
Balduzzi, Adriana [14 ,15 ]
Poetschger, Ulrike [16 ]
Peters [17 ]
Locatelli, Franco [18 ]
机构
[1] Wroclaw Med Univ, Dept Pediat Bone Marrow Transplantat Oncol & Hema, Wroclaw, Poland
[2] Univ Childrens Hosp Frankfurt, Frankfurt, Germany
[3] Univ Hosp Robert Debre, Assistance Publ Hop Paris APHP, Dept Pediat Hematol & Immunol, Paris, France
[4] Charles Univ Prague, Univ Hosp Motol, Dept Pediat Hematol Oncol, Prague, Czech Republic
[5] Oslo Univ Hosp, Dept Pediat Hematol & Oncol, Oslo, Norway
[6] Rigshosp, Copenhagen Univ Hosp, Copenhagen, Denmark
[7] Comenius Univ, Natl Inst Childrens Dis, Dept Pediat Hematol & Oncol, Bone Marrow Transplantat Unit, Bratislava, Slovakia
[8] Schneider Childrens Med Ctr Israel, Dept Hematol Oncol, Petah Tiqwa, Israel
[9] Univ Childrens Hosp, Zurich, Switzerland
[10] Karolinska Univ, Tema Canc, ME Cellterapi Allogen Stamcellstransplantat CAST, Stockholm, Sweden
[11] Hosp Univ Vall dHebron, Vall dHebron Inst Recerca, Barcelona, Spain
[12] Heinrich Heine Univ, Div Pediat Stem Cell Therapy, Dept Pediat Oncol Hematol & Clin Immunol, Med Fac, Dusseldorf, Germany
[13] Hop Univ Geneve, Geneva, Switzerland
[14] Fdn IRCCS San Gerardo de Tintori, Pediat Hematopoiet Transplant Unit, Monza, Italy
[15] Univ Milano Bicocca, Sch Med & Surg, Milan, Italy
[16] St Anna Childrens Canc Res Inst CCRI, Vienna, Austria
[17] St Anna Childrens Hosp, Vienna, Austria
[18] Univ Cattolica Sacro Cuore, Dept Pediat, Rome, Italy
关键词
D O I
10.1182/blood-2023-180728
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页数:5
相关论文
共 6 条
  • [1] Comparable outcomes after busulfan- or treosulfan-based conditioning for allo-HSCT in children with ALL: results of FORUM
    Kalwak, Krzysztof
    Moser, Laura M.
    Poetschger, Ulrike
    Bader, Peter
    Kleinschmidt, Katharina
    Meisel, Roland
    Dalle, Jean-Hugues
    Yesilipek, Akif
    Balduzzi, Adriana
    Krivan, Gergely
    Goussetis, Evgenios
    Staciuk, Raquel
    Sedlacek, Petr
    Pichler, Herbert
    Svec, Peter
    Gabriel, Melissa
    Guengoer, Tayfun
    Bilic, Ernest
    Buechner, Jochen
    Renard, Marleen
    Vettenranta, Kim
    Ifversen, Marianne
    Diaz-de-Heredia, Cristina
    Stein, Jerry
    Toporski, Jacek
    Bierings, Marc
    Peters, Christina
    Ansari, Marc
    Locatelli, Franco
    BLOOD ADVANCES, 2025, 9 (04) : 741 - 751
  • [2] THE RESULTS OF ALLOGENEIC HSCT AFTER TREOSULFAN-BASED CONDITIONING REGIMEN IN CHILDREN WITH AML: MULTICENTER RETROSPECTIVE STUDY OF THE POLISH PEDIATRIC STUDY GROUP FOR HSCT
    Sobkowiak-Sobierajska, Agnieszka
    Zajac-Spychala, Olga
    Deregowski, Maksymilian
    Mielcarek-Siedziuk, Monika
    Kalwak, Krzysztof
    Zaucha-Prazmo, Agnieszka
    Drabko, Katarzyna
    Debski, Robert
    Styczynski, Jan
    Gozdzik, Jolanta
    Wachowiak, Jacek
    BONE MARROW TRANSPLANTATION, 2024, 59 : 264 - 265
  • [3] Relapse Is the Most Common Treatment Failure Post HSCT in Children with ALL below 4 Years of Age Given a Chemo-Based Conditioning Regimen. Results from the Prospective Multinational Forum-Trial
    Peters, Christina
    Poetschger, Ulrike
    Dalle, Jean-Hugues
    Yesilipek, Akif
    Stein, Jerry
    Pichler, Herbert
    Balduzzi, Adriana
    Locatelli, Franco
    Sedlacek, Petr
    Wachowiak, Jacek
    Gungor, Tayfun
    Ifversen, Marianne
    Renard, Marleen
    Truong, Tony H.
    Staciuk, Raquel
    Shaw, Peter J.
    Krivan, Gergely
    Buchner, Jochen
    Bader, Peter
    BLOOD, 2022, 140
  • [4] LOW TOXICITY WITH MYELOABLATIVE CHEMO-BASED CONDITIONING FOR CHILDREN WITH ALL BELOW 4 YEARS OF AGE. RESULTS FROM THE PROSPECTIVE MULTINATIONAL FORUM-TRIAL
    Peters, Christina
    Poetschger, Ulrike
    Dalle, Jean-Hugues
    Yesilipek, Akif
    Stein, Jerry
    Pichler, Herbert
    Balduzzi, Adriana
    Locatelli, Franco
    Sedlacek, Petr
    Wachowiak, Jacek
    Gungor, Tayfun
    Ifversen, Marianne
    Renard, Marleen
    Truong, Tony H.
    Staciuk, Raquel
    Shaw, Peter J.
    Krivan, Gergely
    Buechner, Jochen
    Bader, Peter
    BONE MARROW TRANSPLANTATION, 2023, 58 (SUPP1) : 137 - 138
  • [5] Preliminary results of novel Treosulfan-based conditioning regimen for allogenic HSCT with TCRαβ/CD19 graft depletion in Nijmegen breakage syndrome after five years of Busulfan experience
    Laberko, Alexandra
    Gutovskaya, Elena
    Radigina, Svetlana
    Kozlovskaya, Svetlana
    Shipitsina, Irina
    Deripapa, Elena
    Shcherbina, Anna
    Maschan, Michael
    Maschan, Alexei
    Balashov, Dmitry
    BONE MARROW TRANSPLANTATION, 2018, 53 : 531 - 531
  • [6] Long-Term Data Confirm the Superiority of Total Body Irradiation-Containing Conditioning Regimen in Comparison to a Chemotherapy-Based Preparation in Children with Acute Lymphoblastic Leukemia Above the Age of 4 Years Given an Unmanipulated Allograft. Results of the Forum Randomized Clinical Trial
    Locatelli, Franco
    Bader, Peter
    Dalle, Jean-Hugues
    Poetschger, Ulrike
    Pichler, Herbert
    Sedlacek, Petr
    Buchner, Jochen
    Shaw, Peter J.
    Ifversen, Marianne
    Staciuk, Raquel
    Vettenranta, Kim
    Balduzzi, Adriana
    Peters, Christina
    BLOOD, 2022, 140 : 4865 - 4867