共 50 条
- [2] Onasemnogene Abeparvovec: A Review in Spinal Muscular Atrophy [J]. CNS Drugs, 2022, 36 : 995 - 1005
- [3] Onasemnogene Abeparvovec: A Review in Spinal Muscular Atrophy [J]. CNS DRUGS, 2022, 36 (09) : 995 - 1005
- [8] An evaluation of onasemnogene abeparvovec for spinal muscular atrophy (SMN1) [J]. EXPERT OPINION ON ORPHAN DRUGS, 2021, 9 (7-10): : 199 - 204
- [9] Onasemnogene-abeparvovec administration to premature infants with spinal muscular atrophy [J]. ANNALS OF CLINICAL AND TRANSLATIONAL NEUROLOGY, 2024,